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pro vyhledávání: '"Stephanie L Conway-Allen"'
Publikováno v:
Journal of Child Neurology. 35:348-353
The objective of this review is to summarize the pharmacology, efficacy, and safety of cerliponase alfa for the treatment of late infantile neuronal ceroid lipofuscinosis type 2 (CLN2). Cerliponase alfa is recombinant human tripeptidyl peptidase 1 en