Zobrazeno 1 - 2
of 2
pro vyhledávání: '"Siti Humairah Mohd Rodhi"'
Publikováno v:
International Journal of Molecular Sciences, Vol 25, Iss 15, p 8342 (2024)
Adeno-associated viruses (AAVs) have emerged as promising tools for gene therapy due to their safety and efficacy in delivering therapeutic genes or gene editing sequences to various tissues and organs. AAV serotype 9 (AAV9), among AAV serotypes, sta
Externí odkaz:
https://doaj.org/article/db498de78e5c411999c60f19c3377920
Autor:
Kian Chuan Sia, Shu Uin Gan, Siti Humairah Mohd Rodhi, Zhen Ying Fu, John J. Kopchick, Michael J. Waters, Kok Onn Lee
Publikováno v:
Gene therapy. 29(6)
The only treatment tested for growth hormone receptor (GHR) defective Laron Syndrome (LS) is injections of recombinant insulin-like-growth factor 1 (rhIGF1). The response is suboptimal and associated with progressive obesity. In this study, we treate