Zobrazeno 1 - 10
of 20
pro vyhledávání: '"Samuele Ferrari"'
Autor:
David Bennett, Matteo Fanetti, Maddalena Messina, Barbara Toniella Corradini, Asma Bendjeddou, Samuele Ferrari, Felice Perillo, Luca Luzzi, Piero Paladini, Elena Marchini, Elena Bargagli, Antonella Fossi
Publikováno v:
JHLT Open, Vol 5, Iss , Pp 100106- (2024)
Background: Extracorporeal photopheresis (ECP) is considered an emerging rescue therapy for patients with chronic lung allograft dysfunction (CLAD). The aim of the study was to set up a web-based data collection tool for lung transplant patients with
Externí odkaz:
https://doaj.org/article/ef6a2a8d53bf46e5899ad356ecc0228f
Autor:
Claudia Asperti, Daniele Canarutto, Simona Porcellini, Francesca Sanvito, Francesca Cecere, Valentina Vavassori, Samuele Ferrari, Elisabetta Rovelli, Luisa Albano, Aurelien Jacob, Lucia Sergi Sergi, Elisa Montaldo, Francesca Ferrua, Luis Ignacio González-Granado, Vassilios Lougaris, Raffaele Badolato, Andrea Finocchi, Anna Villa, Marina Radrizzani, Luigi Naldini
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 546-557 (2023)
Hyper-IgM1 is a rare X-linked combined immunodeficiency caused by mutations in the CD40 ligand (CD40LG) gene with a median survival of 25 years, potentially treatable with in situ CD4+ T cell gene editing with Cas9 and a one-size-fits-most corrective
Externí odkaz:
https://doaj.org/article/95bf4664548f487685bff24201e74568
Autor:
Anastasia Conti, Teresa Tavella, Rosaria De Marco, Federico Midena, Samuele Ferrari, Stefano Beretta, Chiara Brombin, Ivan Merelli, Luigi Naldini, Raffaella DI Micco
Publikováno v:
HemaSphere, Vol 7, p e7928137 (2023)
Externí odkaz:
https://doaj.org/article/343c93fe08f64f24810144323ae4bcc7
Autor:
Martina Fiumara, Samuele Ferrari, Attya Omer-Javed, Stefano Beretta, Luisa Albano, Daniele Canarutto, Angelica Varesi, Chiara Gaddoni, Chiara Brombin, Federica Cugnata, Erika Zonari, Matteo Maria Naldini, Matteo Barcella, Bernhard Gentner, Ivan Merelli, Luigi Naldini
Publikováno v:
HemaSphere, Vol 7, p e6237653 (2023)
Externí odkaz:
https://doaj.org/article/4dacf51b000c4c6baa7cbba5fcb5b5e7
Autor:
Daniele Canarutto, Claudia Asperti, Valentina Vavassori, Simona Porcellini, Elisabetta Rovelli, Marianna Paulis, Samuele Ferrari, Tiziana Plati, Lucia Sergi Sergi, Anna Villa, Marina Radrizzani, Luigi Naldini
Publikováno v:
HemaSphere, Vol 7, p e6715437 (2023)
Externí odkaz:
https://doaj.org/article/bc9d4c9418754b6698f01cbb046d797d
Autor:
Luigi Vetrugno, Daniele Orso, Francesco Corradi, Gianluca Zani, Savino Spadaro, Francesco Meroi, Natascia D’Andrea, Tiziana Bove, Gianmaria Cammarota, Edoardo De Robertis, Samuele Ferrari, Marcello Guarnieri, Margherita Ajuti, Maurizio Fusari, Domenico Luca Grieco, Cristian Deana, Enrico Boero, Federico Franchi, Sabino Scolletta, Salvatore Maurizio Maggiore, Francesco Forfori
Publikováno v:
Respiratory Research, Vol 23, Iss 1, Pp 1-7 (2022)
Abstract Background Diaphragmatic dysfunction is a major factor responsible for weaning failure in patients that underwent prolonged invasive mechanical ventilation for acute severe respiratory failure from COVID-19. This study hypothesizes that ultr
Externí odkaz:
https://doaj.org/article/0064a3327e0f44daac29ff8b55d10e1d
Autor:
Samuele Ferrari, Valentina Vavassori, Daniele Canarutto, Aurelien Jacob, Maria Carmina Castiello, Attya Omer Javed, Pietro Genovese
Publikováno v:
Frontiers in Genome Editing, Vol 3 (2021)
In the field of hematology, gene therapies based on integrating vectors have reached outstanding results for a number of human diseases. With the advent of novel programmable nucleases, such as CRISPR/Cas9, it has been possible to expand the applicat
Externí odkaz:
https://doaj.org/article/b32545ce26e24840b29d5b4f310a9104
Autor:
Samuele Ferrari, Erika Valeri, Anastasia Conti, Serena Scala, Annamaria Aprile, Raffaella Di Micco, Anna Kajaste-Rudnitski, Eugenio Montini, Giuliana Ferrari, Alessandro Aiuti, Luigi Naldini
Publikováno v:
Cell Stem Cell. 30:549-570
Publikováno v:
Seminars in Immunology. 66:101731
Autor:
Samuele Ferrari, Aurelien Jacob, Daniela Cesana, Marianne Laugel, Stefano Beretta, Angelica Varesi, Giulia Unali, Anastasia Conti, Daniele Canarutto, Luisa Albano, Andrea Calabria, Valentina Vavassori, Carlo Cipriani, Maria Carmina Castiello, Simona Esposito, Chiara Brombin, Federica Cugnata, Oumeya Adjali, Eduard Ayuso, Ivan Merelli, Anna Villa, Raffaella Di Micco, Anna Kajaste-Rudnitski, Eugenio Montini, Magalie Penaud-Budloo, Luigi Naldini
Publikováno v:
Cell stem cell. 29(10)
Long-range gene editing by homology-directed repair (HDR) in hematopoietic stem/progenitor cells (HSPCs) often relies on viral transduction with recombinant adeno-associated viral vector (AAV) for template delivery. Here, we uncover unexpected load a