Zobrazeno 1 - 10
of 1 465
pro vyhledávání: '"S. Chamberlain"'
Autor:
A.R. Dores, I. Carvalho, J. Burkauskas, V. Beretta, K. Ioannidis, P. Simonato, A. Gomez, Z. Demetrovics, H. Fujiwara, S. Chamberlain, N. Fineberg, F. Barbosa, O. Corazza
Publikováno v:
European Psychiatry, Vol 64, Pp S290-S291 (2021)
Introduction The Coronavirus pandemic has originated unprecedented sanitary control measures that have conditioned people’s lifestyles and habits. Little is known about the impact of such measures, especially the most restrictive, on recent and gro
Externí odkaz:
https://doaj.org/article/30bcc874cc314e008fcd47a59cb5fc65
Autor:
S.W. Nelson, U. Stolz, B.A. Dreifuss, S. Chamberlain, H.S. Hammerstedt, B. Alfunsi, M. Bisanzo
Publikováno v:
Annals of Global Health, Vol 80, Iss 3 (2014)
Externí odkaz:
https://doaj.org/article/1fdee256d218458c85a6c0093570d5c1
Autor:
B. Dreifuss, U. Periyanayagam, S. Chamberlain, S.W. Nelson, H. Hammerstedt, J. Kamugisha, M. Bisanzo
Publikováno v:
Annals of Global Health, Vol 81, Iss 1, Pp 146-147 (2015)
Externí odkaz:
https://doaj.org/article/068a959f41bf47fc95e34a83adc43780
Autor:
Domagoj Cikes, Kareem Elsayad, Erdinc Sezgin, Erika Koitai, Ferenc Torma, Michael Orthofer, Rebecca Yarwood, Leonhard X. Heinz, Vitaly Sedlyarov, Nasser Darwish Miranda, Adrian Taylor, Sophie Grapentine, Fathiya al-Murshedi, Anne Abot, Adelheid Weidinger, Candice Kutchukian, Colline Sanchez, Shane J. F. Cronin, Maria Novatchkova, Anoop Kavirayani, Thomas Schuetz, Bernhard Haubner, Lisa Haas, Astrid Hagelkruys, Suzanne Jackowski, Andrey V. Kozlov, Vincent Jacquemond, Claude Knauf, Giulio Superti-Furga, Eric Rullman, Thomas Gustafsson, John McDermot, Martin Lowe, Zsolt Radak, Jeffrey S. Chamberlain, Marica Bakovic, Siddharth Banka, Josef M. Penninger
Publikováno v:
Nature Metabolism. 5:495-515
Autor:
Arden B. Piepho, Jeovanna Lowe, Laurel R. Cumby, Lisa E. Dorn, Dana M. Lake, Neha Rastogi, Megan D. Gertzen, Sarah L. Sturgill, Guy L. Odom, Mark T. Ziolo, Federica Accornero, Jeffrey S. Chamberlain, Jill A. Rafael-Fortney
Publikováno v:
Molecular Therapy - Methods & Clinical Development. 28:344-354
Autor:
Jessica F, Boehler, Kristy J, Brown, Margaret, Beatka, J Patrick, Gonzalez, Roxana, Donisa Dreghici, Meghan, Soustek-Kramer, Sharon, McGonigle, Annie, Ganot, Timothy, Palmer, Caitlin, Lowie, Jeffrey S, Chamberlain, Michael W, Lawlor, Carl A, Morris
Publikováno v:
Neuromuscular Disorders. 33:40-49
Accelerated approval based on a likely surrogate endpoint can be life-changing for patients suffering from a rare progressive disease with unmet medical need, as it substantially hastens access to potentially lifesaving therapies. In one such example
Autor:
Jeffrey S. Chamberlain, Melissa Robb, Serge Braun, Kristy J. Brown, Olivier Danos, Annie Ganot, Pedro Gonzalez-Alegre, Nina Hunter, Craig McDonald, Carl Morris, Mark Tobolowsky, Kathryn R. Wagner, Olivia Ziolkowski, Dongsheng Duan
Publikováno v:
Human gene therapy, vol 34, iss 9-10
Duchenne muscular dystrophy (DMD) is a serious, rare genetic disease, affecting primarily boys. It is caused by mutations in the DMD gene and is characterized by progressive muscle degeneration that results in loss of function and early death due to
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::d4cd9d835233f4a077af22bfee836cfc
https://escholarship.org/uc/item/0v56c0vk
https://escholarship.org/uc/item/0v56c0vk
Autor:
Chady H. Hakim, Nalinda B. Wasala, Xiufang Pan, Kasun Kodippili, Yongping Yue, Keqing Zhang, Gang Yao, Brittney Haffner, Sean X. Duan, Julian Ramos, Joel S. Schneider, N. Nora Yang, Jeffrey S. Chamberlain, Dongsheng Duan
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 216-230 (2017)
Micro-dystrophins are highly promising candidates for treating Duchenne muscular dystrophy, a lethal muscle disease caused by dystrophin deficiency. Here, we report robust disease rescue in the severe DBA/2J-mdx model with a neuronal nitric oxide syn
Externí odkaz:
https://doaj.org/article/a968d82e3a484f8cb6cd48ebc8ad7bec
Autor:
Sajedah M. Hindi, Michael J. Petrany, Elena Greenfeld, Leah C. Focke, Alyssa A.W. Cramer, Michael A. Whitt, Vikram Prasad, Jeffrey S. Chamberlain, Benjamin Podbilewicz, Douglas P. Millay
Publikováno v:
bioRxiv
SummaryEntry of enveloped viruses into cells is mediated by fusogenic proteins that form a complex between membranes to drive rearrangements needed for fusion. Skeletal muscle development also requires membrane fusion events between progenitor cells
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::88b91a4a4ddb2a88c9938b3657a89b83
https://europepmc.org/articles/PMC10055243/
https://europepmc.org/articles/PMC10055243/
Akademický článek
Tento výsledek nelze pro nepřihlášené uživatele zobrazit.
K zobrazení výsledku je třeba se přihlásit.
K zobrazení výsledku je třeba se přihlásit.