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Autor:
F Cappelli, P Kale, M Maurer, M Fontana, M Grogan, F Fernandes, T Palacek, M Taylor, R Hung, A González–duarte, S Puolsen, E Donal, F Perfetto, K Tsujita, W Yu, N Sarswat, M White, E Yureneva, P Jay, J Vest, J Gillmore
Publikováno v:
European Heart Journal Supplements. 25:D181-D182
Introduction Transthyretin–mediated (ATTR) amyloidosis is a progressive and fatal disease. Patients with hereditary or wild–type ATTR amyloidosis frequently develop cardiomyopathy (CM). Patisiran, an IV RNAi therapeutic that inhibits synthesis of