Zobrazeno 1 - 5
of 5
pro vyhledávání: '"Riling CR"'
Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates.
Autor:
Costa-Verdera H; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France.; Sorbonne University Paris and INSERM U974, 75013, Paris, France., Collaud F; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Riling CR; Spark Therapeutics, Philadelphia, PA, 19104, USA., Sellier P; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Nordin JML; Spark Therapeutics, Philadelphia, PA, 19104, USA., Preston GM; Spark Therapeutics, Philadelphia, PA, 19104, USA., Cagin U; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Fabregue J; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Barral S; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Moya-Nilges M; Pasteur Institute, 75015, Paris, France., Krijnse-Locker J; Pasteur Institute, 75015, Paris, France., van Wittenberghe L; Genethon, 91000, Evry, France., Daniele N; Genethon, 91000, Evry, France., Gjata B; Genethon, 91000, Evry, France., Cosette J; Genethon, 91000, Evry, France., Abad C; Université de Rouen Normandie-IRIB, 76183, Rouen, France., Simon-Sola M; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Charles S; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Li M; Spark Therapeutics, Philadelphia, PA, 19104, USA., Crosariol M; Spark Therapeutics, Philadelphia, PA, 19104, USA., Antrilli T; Spark Therapeutics, Philadelphia, PA, 19104, USA., Quinn WJ 3rd; Spark Therapeutics, Philadelphia, PA, 19104, USA., Gross DA; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Boyer O; Université de Rouen Normandie-IRIB, 76183, Rouen, France., Anguela XM; Spark Therapeutics, Philadelphia, PA, 19104, USA., Armour SM; Spark Therapeutics, Philadelphia, PA, 19104, USA., Colella P; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Ronzitti G; Genethon, 91000, Evry, France.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France., Mingozzi F; Genethon, 91000, Evry, France. Federico.mingozzi@sparktx.com.; Université Paris-Saclay, Univ Evry, Inserm, Integrare research Unit UMR_S951, 91000, Evry, France. Federico.mingozzi@sparktx.com.; Sorbonne University Paris and INSERM U974, 75013, Paris, France. Federico.mingozzi@sparktx.com.; Spark Therapeutics, Philadelphia, PA, 19104, USA. Federico.mingozzi@sparktx.com.
Publikováno v:
Nature communications [Nat Commun] 2021 Nov 04; Vol. 12 (1), pp. 6393. Date of Electronic Publication: 2021 Nov 04.
Autor:
Lv K; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Jiang J; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Donaghy R; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Riling CR; Progenra, Inc., Malvern, Pennsylvania 19355, USA., Cheng Y; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Chandra V; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Rozenova K; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., An W; Eppley Institute for Research in Cancer and Allied Diseases, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA.; Department of Genetics, Cell Biology, and Anatomy, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA., Mohapatra BC; Eppley Institute for Research in Cancer and Allied Diseases, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA.; Department of Genetics, Cell Biology, and Anatomy, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA., Goetz BT; Eppley Institute for Research in Cancer and Allied Diseases, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA.; Department of Genetics, Cell Biology, and Anatomy, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA., Pillai V; Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA., Han X; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Todd EA; Progenra, Inc., Malvern, Pennsylvania 19355, USA., Jeschke GR; Division of Hematology and Oncology, Abramson Cancer Center, University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Langdon WY; School of Pathology and Laboratory Medicine, University of Western Australia, Crawley, Western Australia 6009, Australia., Kumar S; Progenra, Inc., Malvern, Pennsylvania 19355, USA., Hexner EO; Division of Hematology and Oncology, Abramson Cancer Center, University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Band H; Eppley Institute for Research in Cancer and Allied Diseases, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA.; Department of Genetics, Cell Biology, and Anatomy, University of Nebraska Medical Center, Omaha, Nebraska 6819, USA., Tong W; Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA.
Publikováno v:
Genes & development [Genes Dev] 2017 May 15; Vol. 31 (10), pp. 1007-1023. Date of Electronic Publication: 2017 Jun 13.
Autor:
O'Leary CE; Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Riling CR; Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA., Spruce LA; Department of Pathology and Laboratory Medicine, Cell Pathology Division, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA., Ding H; Department of Pathology and Laboratory Medicine, Cell Pathology Division, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA., Kumar S; Progenra Inc, Malvern, Pennsylvania, 19355, USA., Deng G; Department of Pathology and Laboratory Medicine, Cell Pathology Division, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA., Liu Y; Department of Pediatrics, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA., Seeholzer SH; Department of Pathology and Laboratory Medicine, Cell Pathology Division, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA., Oliver PM; Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA.; Department of Pathology and Laboratory Medicine, Cell Pathology Division, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.
Publikováno v:
Nature communications [Nat Commun] 2016 Apr 18; Vol. 7, pp. 11226. Date of Electronic Publication: 2016 Apr 18.
Autor:
Beal AM; Cell Pathology Division, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA., Ramos-Hernández N, Riling CR, Nowelsky EA, Oliver PM
Publikováno v:
Nature immunology [Nat Immunol] 2011 Nov 13; Vol. 13 (1), pp. 77-85. Date of Electronic Publication: 2011 Nov 13.
Autor:
Ramon HE; University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA., Riling CR, Bradfield J, Yang B, Hakonarson H, Oliver PM
Publikováno v:
Mucosal immunology [Mucosal Immunol] 2011 May; Vol. 4 (3), pp. 314-24. Date of Electronic Publication: 2010 Oct 20.