Rycal S48168 (ARM210) for RYR1 -related myopathies: a phase one, open-label, dose-escalation trial.

Autor: Todd JJ; Neuromuscular and Neurogenetic Disorders of Childhood Section, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA.; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA.; Clinical Trials Unit, National Institute of Neurological Disorders and Stroke, Bethesda, MD, USA., Lawal TA; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA., Chrismer IC; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA., Kokkinis A; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA., Grunseich C; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA., Jain MS; Mark O. Hatfield Clinical Research Center, Rehabilitation Medicine Department, National Institutes of Health, Bethesda, MD 20814, USA., Waite MR; Mark O. Hatfield Clinical Research Center, Rehabilitation Medicine Department, National Institutes of Health, Bethesda, MD 20814, USA., Biancavilla V; Mark O. Hatfield Clinical Research Center, Rehabilitation Medicine Department, National Institutes of Health, Bethesda, MD 20814, USA., Pocock S; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA., Brooks K; Neuromuscular and Neurogenetic Disorders of Childhood Section, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA.; Clinical Trials Unit, National Institute of Neurological Disorders and Stroke, Bethesda, MD, USA., Mendoza CJ; Neuromuscular and Neurogenetic Disorders of Childhood Section, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA., Norato G; Clinical Trials Unit, National Institute of Neurological Disorders and Stroke, Bethesda, MD, USA., Cheung K; Mailman School of Public Health, Columbia University, NY 10032, USA., Riekhof W; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA., Varma P; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA., Colina-Prisco C; Section of Sensory Science and Metabolism, National Institute on Alcohol Abuse and Alcoholism, National Institutes of Health, Bethesda, MD 20814, USA., Emile-Backer M; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA., Meilleur KG; National Institute of Nursing Research, National Institutes of Health, Bethesda, MD 20814, USA., Marks AR; Department of Physiology and Cellular Biophysics, Columbia University Vagelos College of Physicians and Surgeons, New York, NY 10032, USA., Webb Y; ARMGO Pharma, Inc, Ardsley, NY 10591, USA., Marcantonio EE; ARMGO Pharma, Inc, Ardsley, NY 10591, USA., Foley AR; Neuromuscular and Neurogenetic Disorders of Childhood Section, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA., Bönnemann CG; Neuromuscular and Neurogenetic Disorders of Childhood Section, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA., Mohassel P; Neuromuscular and Neurogenetic Disorders of Childhood Section, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20814, USA.

Publikováno v: EClinicalMedicine [EClinicalMedicine] 2024 Jan 25; Vol. 68, pp. 102433. Date of Electronic Publication: 2024 Jan 25 (Print Publication: 2024).

P.09 Comprehensive database for RYR1-related disorders: concept and progress update

Autor: Lawal, T., Riekhof, W., Goldberg, M., Kushnir, A., Terry, N., Marks, A., Todd, J.

Publikováno v: In Neuromuscular Disorders October 2022 32 Supplement 1:S46-S46

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Micafungin-Induced Cell Wall Damage Stimulates Morphological Changes Consistent with Microcycle Conidiation in Aspergillus nidulans .

Autor: Reese S; School of Biological Sciences, University of Nebraska, Lincoln, NE 68503, USA., Chelius C; Biologics Development, Global Product Development and Supply, Bristol Myers Squibb Company, Devens, MA 01434, USA., Riekhof W; School of Biological Sciences, University of Nebraska, Lincoln, NE 68503, USA., Marten MR; Department of Chemical, Biochemical and Environmental Engineering, University of Maryland Baltimore County, Baltimore, MD 21250, USA., Harris SD; Department of Plant Pathology and Microbiology and Department of Entomology, Iowa State University, Ames, IA 50011, USA.

Publikováno v: Journal of fungi (Basel, Switzerland) [J Fungi (Basel)] 2021 Jun 29; Vol. 7 (7). Date of Electronic Publication: 2021 Jun 29.

Using flux theory in dynamic omics data sets to identify differentially changing signals using DPoP.

Autor: Edwards, Harley¹ (AUTHOR), Zavorskas, Joseph² (AUTHOR), Huso, Walker¹ (AUTHOR), Doan, Alexander G.¹ (AUTHOR), Silbiger, Caton¹ (AUTHOR), Harris, Steven³ (AUTHOR), Srivastava, Ranjan^2,4 (AUTHOR), Marten, Mark R.¹ (AUTHOR) marten@umbc.edu

Publikováno v: BMC Bioinformatics. 9/27/2024, Vol. 25 Issue 1, p1-20. 20p.