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of 2
pro vyhledávání: '"Richard Lemons"'
Autor:
Richard Lemons, Michael Wang, Julie Curtin, Lynda Mae Lepatan, Christoph Male, Flora Peyvandi, Mario von Depka Prondzinski, Rongrong Wang, William McKeand, Wilfried Seifert, Johannes Oldenburg
Publikováno v:
TH Open, Vol 08, Iss 01, Pp e155-e163 (2024)
Introduction Recombinant fusion protein linking coagulation factor IX (FIX) with albumin (rIX-FP) has been shown to be an effective, well-tolerated treatment for patients with severe hemophilia B who had previously received factor replacement therapy
Externí odkaz:
https://doaj.org/article/9b8f1fd5ab434c34948cf4c09b501cde
Autor:
Steven W. Pipe, Frank W.G. Leebeek, Michael Recht, Nigel S. Key, Giancarlo Castaman, Wolfgang Miesbach, Susan Lattimore, Kathelijne Peerlinck, Paul Van der Valk, Michiel Coppens, Peter Kampmann, Karina Meijer, Niamh O’Connell, K. John Pasi, Daniel P. Hart, Rashid Kazmi, Jan Astermark, Cedric R.J.R. Hermans, Robert Klamroth, Richard Lemons, Nathan Visweshwar, Annette von Drygalski, Guy Young, Shelley E. Crary, Miguel Escobar, Esteban Gomez, Rebecca Kruse-Jarres, Doris V. Quon, Emily Symington, Michael Wang, Allison P. Wheeler, Robert Gut, Ying P. Liu, Ricardo E. Dolmetsch, David L. Cooper, Yanyan Li, Brahm Goldstein, Paul E. Monahan
Publikováno v:
New England journal of medicine, 388(8), 706-718. Massachussetts Medical Society
New England Journal of Medicine, 388(8), 706-718. MASSACHUSETTS MEDICAL SOC
New England Journal of Medicine, 388(8), 706-718. Massachussetts Medical Society
New England Journal of Medicine, 388(8), 706-718. MASSACHUSETTS MEDICAL SOC
New England Journal of Medicine, 388(8), 706-718. Massachussetts Medical Society
Background: Moderate-to-severe hemophilia B is treated with lifelong, continuous coagulation factor IX replacement to prevent bleeding. Gene therapy for hemophilia B aims to establish sustained factor IX activity, thereby protecting against bleeding