The STArgardt Remofuscin Treatment Trial (STARTT): design and baseline characteristics of enrolled Stargardt patients

Autor: Dhooge, Patty P.A., Möller, Philipp T., Boon, Camiel J.F., Lotery, Andrew J., Herrmann, Philipp, Battaglia Parodi, Maurizio, Klein, Wolfgang, Fsadni, Mario G., Wheeler-Schilling, Thomas H., Jungmann, Oliver, Müller, Hans, Holz, Frank G., Schmitz-Valckenberg, Steffen, Peters, Tobias M., Stingl, Katarina, Hoyng, Carel B., Soraprazan Consortium

Background: This report describes the study design and baseline characteristics of patients with Stargardt disease (STGD1) enrolled in the STArgardt Remofuscin Treatment Trial (STARTT). Methods: In total, 87 patients with genetically confirmed STGD1

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::5fe4484cab3ac73b6b1466bf189d5967
https://zenodo.org/record/7122963

The STArgardt Remofuscin Treatment Trial (STARTT): design and baseline characteristics of enrolled Stargardt patients

Autor: Steffen Schmitz-Valckenberg, Oliver Jungmann, Frank G. Holz, Camiel J. F. Boon, Philipp Herrmann, Katarina Stingl, Wolfgang Klein, Andrew J. Lotery, Carel B. Hoyng, Patty P.A. Dhooge, Thomas H. Wheeler-Schilling, Hans H. Müller, Maurizio Battaglia Parodi, Tobias Peters, Philipp T. Möller, Mario G. Fsadni

Publikováno v: Open Research Europe
Open Research Europe, 1:96
Open Research Europe, 1

Background: This report describes the study design and baseline characteristics of patients with Stargardt disease (STGD1) enrolled in the STArgardt Remofuscin Treatment Trial (STARTT). Methods: In total, 87 patients with genetically confirmed STGD1

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2fefb515501f86ce7a464cfe964239b3
https://doi.org/10.12688/openreseurope.13872.1

The STArgardt Remofuscin Treatment Trial (STARTT): design and baseline characteristics of enrolled Stargardt patients.

Autor: Dhooge PPA; Department of Ophthalmology, Radboud University Nijmegen Medical Centre, Nijmegen, 6500HB, The Netherlands.; Donders Institute for Brain, Cognition and Behaviour, Nijmegen, 6525EN, The Netherlands., Möller PT; GRADE reading center, Bonn, 53127, Germany.; Department of Ophthalmology, University of Bonn, Bonn, 53127, Germany., Boon CJF; Department of Ophthalmology, Amsterdam University Medical Center, Amsterdam, 1081HV, The Netherlands.; Department of Ophthalmology, Leiden University Medical Center, Leiden, 2333ZA, The Netherlands., Lotery AJ; Faculty of Medicine, University of Southampton, Southampton, SO17 1BJ, UK., Herrmann P; Department of Ophthalmology, University of Bonn, Bonn, 53127, Germany.; Center for Rare Diseases Bonn (ZSEB), University of Bonn, Bonn, 53113, Germany., Battaglia Parodi M; Department of Ophthalmology, Ospedale San Raffaele, Milan, 20132, Italy., Klein W; Katairo GmbH, Kusterdingen, 72127, Germany., Fsadni MG; Katairo GmbH, Kusterdingen, 72127, Germany.; International Pharm-Med Ltd, Hemel Hempstead, HP1 1LD, UK., Wheeler-Schilling TH; University Eye Hospital, Center for Ophthalmology, Institute for Ophthalmic Research, University of Tübingen, Tübingen, 72076, Germany., Jungmann O; Smerud Medical Research Germany GmbH, Mannheim, D-68161, Germany., Müller H; Smerud Medical Research Germany GmbH, Mannheim, D-68161, Germany., Holz FG; GRADE reading center, Bonn, 53127, Germany.; Department of Ophthalmology, University of Bonn, Bonn, 53127, Germany., Schmitz-Valckenberg S; GRADE reading center, Bonn, 53127, Germany.; Department of Ophthalmology, University of Bonn, Bonn, 53127, Germany.; John A. Moran Eye Center, University of Utah, Salt Lake City, Utah, 84132, USA., Peters TM; University Eye Hospital, Center for Ophthalmology, Institute for Ophthalmic Research, University of Tübingen, Tübingen, 72076, Germany., Stingl K; University Eye Hospital, Center for Ophthalmology, Institute for Ophthalmic Research, University of Tübingen, Tübingen, 72076, Germany.; Center for Rare Eye Diseases, University of Tübingen, Tübingen, 72076, Germany., Hoyng CB; Department of Ophthalmology, Radboud University Nijmegen Medical Centre, Nijmegen, 6500HB, The Netherlands.; Donders Institute for Brain, Cognition and Behaviour, Nijmegen, 6525EN, The Netherlands.

Publikováno v: Open research Europe [Open Res Eur] 2022 Sep 27; Vol. 1, pp. 96. Date of Electronic Publication: 2022 Sep 27 (Print Publication: 2021).