Zobrazeno 1 - 7
of 7
pro vyhledávání: '"Regina Tayag"'
Publikováno v:
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-6 (2019)
Abstract Background The objective of this study is to describe variations in the healthcare resource utilization (HRU) among individuals with Angelman syndrome (AS) over the first 12 years of life. Data for this study were drawn from the AS Natural H
Externí odkaz:
https://doaj.org/article/1eb922d2e3fc4a288886e64cf1dfa4a0
Publikováno v:
Molecular Genetics & Genomic Medicine, Vol 7, Iss 7, Pp n/a-n/a (2019)
Abstract Background The objective of this study is to describe healthcare resource utilization (HRU) and supportive therapy utilization (STU) among individuals with Angelman syndrome (AS), and to compare such usage by molecular etiology. Methods Part
Externí odkaz:
https://doaj.org/article/c6b3ea264c324a329009795bcd230556
Publikováno v:
Orphanet Journal of Rare Diseases
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-6 (2019)
Orphanet journal of rare diseases, vol 14, iss 1
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-6 (2019)
Orphanet journal of rare diseases, vol 14, iss 1
BackgroundThe objective of this study is to describe variations in the healthcare resource utilization (HRU) among individuals with Angelman syndrome (AS) over the first 12 years of life. Data for this study were drawn from the AS Natural History stu
Publikováno v:
Molecular Genetics & Genomic Medicine
Molecular genetics & genomic medicine, vol 7, iss 7
Molecular Genetics & Genomic Medicine, Vol 7, Iss 7, Pp n/a-n/a (2019)
Molecular genetics & genomic medicine, vol 7, iss 7
Molecular Genetics & Genomic Medicine, Vol 7, Iss 7, Pp n/a-n/a (2019)
Author(s): Khan, Nasreen; Cabo, Raquel; Tan, Wen-Hann; Tayag, Regina; Bird, Lynne M | Abstract: BackgroundThe objective of this study is to describe healthcare resource utilization (HRU) and supportive therapy utilization (STU) among individuals with
Autor:
Seymour Packman, M. Judith Peterschmitt, Atul Mehta, Manisha Balwani, Sarit Assouline, Gregory M. Pastores, Milan Petakov, Hagit N. Baris, Elena Lukina, Suma P. Shankar, Sebastiaan J.M. Gaemers, Hadhami Ben Turkia, Pramod K. Mistry, Andres Ortega, Sumita Danda, Evgueniy Hadjiev, Regina Tayag, Marwan Ghosn
Publikováno v:
American journal of hematology, vol 92, iss 11
Mistry, PK; Lukina, E; Ben Turkia, H; Shankar, SP; Baris, H; Ghosn, M; et al.(2017). Outcomes after 18 months of eliglustat therapy in treatment-naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trial. American Journal of Hematology, 92(11), 1170-1176. doi: 10.1002/ajh.24877. UC Davis: Retrieved from: http://www.escholarship.org/uc/item/3vt8j9ht
American Journal of Hematology
Mistry, PK; Lukina, E; Ben Turkia, H; Shankar, SP; Baris, H; Ghosn, M; et al.(2017). Outcomes after 18 months of eliglustat therapy in treatment-naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trial. American Journal of Hematology, 92(11), 1170-1176. doi: 10.1002/ajh.24877. UC Davis: Retrieved from: http://www.escholarship.org/uc/item/3vt8j9ht
American Journal of Hematology
© 2017 The Authors American Journal of Hematology Published by Wiley Periodicals, Inc. Eliglustat, an oral substrate reduction therapy, is a first-line treatment for adults with Gaucher disease type 1 (GD1) who are poor, intermediate, or extensive C
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f1091112858d13d4efae1ef53bf3f518
https://escholarship.org/uc/item/3vt8j9ht
https://escholarship.org/uc/item/3vt8j9ht
Autor:
Amal El-Beshlawy, Ana Maria Martins, Renata Cravo, Sebastiaan J.M. Gaemers, M. Judith Peterschmitt, Guillermo Drelichman, Timothy M. Cox, Ozlem Goker-Alpan, Elena Lukina, Barry E. Rosenbloom, Manisha Balwani, Thomas A. Burrow, Regina Tayag, Maria Lucia Alves Pedroso, Priya S. Kishnani, Nora Watman
In the phase 3 Study of Eliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease Who Have Reached Therapeutic Goals With Enzyme Replacement Therapy (ENCORE), at 1 year, eliglustat was noninferior to imiglucerase enzyme therapy in maintainin
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e29f459cc07cfd59247d00312a84f24d
Autor:
Elena Lukina, Sebastiaan J.M. Gaemers, Guillermo Drelichman, Regina Tayag, Timothy M. Cox, Audrey W. Hou, M. Judith Peterschmitt, Neal J. Weinreb
Publikováno v:
Molecular Genetics and Metabolism. 120:S37-S38