Zobrazeno 1 - 10
of 14
pro vyhledávání: '"Regina Horneff"'
Publikováno v:
International Journal of Molecular Sciences, Vol 25, Iss 17, p 9477 (2024)
Paroxysmal nocturnal hemoglobinuria (PNH) is a rare and potentially life-threatening hematologic disorder caused by a somatic mutation in a relevant portion of hematopoietic stem cells. Mutation of the phosphatidylinositol glycan biosynthesis class A
Externí odkaz:
https://doaj.org/article/5cc94dede1a54d24803c5aab152ac612
Autor:
Jeff Szer, Jens Panse, Austin Kulasekararaj, Monika Oliver, Bruno Fattizzo, Jun-ichi Nishimura, Regina Horneff, Johan Szamosi, Régis Peffault de Latour
Publikováno v:
International Journal of Molecular Sciences, Vol 25, Iss 16, p 8591 (2024)
Paroxysmal nocturnal haemoglobinuria (PNH) is a rare, potentially life-threatening haematological disease characterised by chronic complement-mediated haemolysis with multiple clinical consequences that impair quality of life. This post hoc analysis
Externí odkaz:
https://doaj.org/article/8eab5b9b8dbb48139158e54fbd498f65
Publikováno v:
International Journal of Molecular Sciences, Vol 25, Iss 16, p 8698 (2024)
Paroxysmal nocturnal hemoglobinuria (PNH) is a rare disease characterized by complement-mediated hemolysis and potentially life-threatening complications. Pegcetacoplan, an inhibitor of complement components C3 and C3b, was approved by the US Food an
Externí odkaz:
https://doaj.org/article/7aeeca49a9114374b7498a9799046901
Autor:
Jeff Szer, Jens Panse, Austin Kulasekararaj, Monika Oliver, Bruno Fattizzo, Jun-Ichi Nishimura, Johan Szamosi, Regina Horneff, Régis Peffault de Latour
Publikováno v:
HemaSphere, Vol 7, p e58190a6 (2023)
Externí odkaz:
https://doaj.org/article/39d770798fe441879f71e2ca590ee6db
Autor:
Richard Kelly, Hisakazu Nishimori, Regina Horneff, Peter Hillmen, Jessica Savage, Mohammed Al-Adhami, Stacie Lallier, Gloria Gerber
Publikováno v:
HemaSphere, Vol 7, p e66610c4 (2023)
Externí odkaz:
https://doaj.org/article/45057cbce2b34ab3b9c8abb2425525ca
Autor:
Régis Peffault de Latour, Jeff Szer, Austin Kulasekararaj, Anna Gaya, Simona Sica, Matthias Nölte, Regina Horneff, Lethagen Stefan
Publikováno v:
HemaSphere, Vol 7, p e36410cc (2023)
Externí odkaz:
https://doaj.org/article/868d681f71714c46932081eade45a3c7
Autor:
Christopher J. Patriquin, Andrija Bogdanovic, Morag Griffin, Richard Kelly, Jaroslaw P. Maciejewski, Brian Mulherin, Régis Peffault de Latour, Alexander Roeth, Veena Selvaratnam, Jeffrey Szer, Jessica Savage, Regina Horneff, Lisa Tan, Michael Yeh, Jens Panse
Publikováno v:
Blood. 140:2921-2923
Autor:
Morag Griffin, Richard Kelly, Dries Deeren, Yeow Tee Goh, Eric Tse, Kensuke Usuki, Raymond Wong, Regina Horneff, Lisa Tan, Michael Yeh, Jessica Savage, Jeff Szer
Publikováno v:
Blood. 140:2937-2939
Autor:
Jens Panse, Koo Wilson, Jesse Fishman, Piotr Wojciechowski, Marlena Wdowiak, Regina Horneff, Christopher J. Patriquin, Monika Oliver, Zalmai Hakimi
Publikováno v:
European Journal of Haematology.
Publikováno v:
Blood. 140:11447-11448