The Challenge of Gene Therapy for Neurological Diseases: Strategies and Tools to Achieve Efficient Delivery to the Central Nervous System

Autor: Guillaume Wurtz, Michel Zerah, Emilie Audouard, Françoise Piguet, Arthur André, Timothée de Saint Denis, Raphael Schatz, Nathalie Cartier, Caroline Sevin, Sandro Alves, Kevin Beccaria

Publikováno v: Human Gene Therapy
Human Gene Therapy, 2021, 32 (7-8), pp.349-374. ⟨10.1089/hum.2020.105⟩
Human Gene Therapy, Mary Ann Liebert, 2021, 32 (7-8), pp.349-374. ⟨10.1089/hum.2020.105⟩

International audience; For more than ten years, gene therapy for neurological diseases has experienced intensive research growth and more recently therapeutic interventions for multiple indicationsBeneficial results in several phase 1/2 clinical stu

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e135e295cc8ada193184c0465b367996
https://doi.org/10.1089/hum.2020.105