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pro vyhledávání: '"Ramon González-Rioja"'
The development of highly dense highly protected surfactant ionizable lipid RNA loaded nanoparticles
Publikováno v:
Frontiers in Immunology, Vol 14 (2023)
The long quest for efficient drug administration has been looking for a universal carrier that can precisely transport traditional drugs, new genomic and proteic therapeutic agents. Today, researchers have found conditions to overcome the two main dr
Externí odkaz:
https://doaj.org/article/10163956c45542e38ad1a190a21b15f6
Autor:
Santi Sala, Irina Portnaya, Patricia Cámara-Sánchez, Jeppe Lyngsø, José Luis Corchero, Natalia García-Aranda, Ibane Abasolo, Josep Merlo-Mas, Edgar Cristóbal-Lecina, Daniel Pulido, Simó Schwartz, Alba Córdoba, Jan Skov Pedersen, Dganit Danino, Judit Tomsen-Melero, Ramon González-Rioja, Solène Passemard, Nora Ventosa, Zamira V. Díaz-Riascos, Elisabet González-Mira, Miriam Royo, Jannik Nedergaard Pedersen, Jaume Veciana, Inbal Abutbul Ionita
Publikováno v:
ACS Applied Materials & Interfaces
Tomsen-Melero, J, Passemard, S, García-Aranda, N, Días-Riascos, Z V, González-Rioja, R, Pedersen, J N, Lyngsø, J, Merlo-Mas, J, Cristóbal-Lecina, E, Corchero, J L, Pulido, D, Cámara-Sánchez, P, Portnaya, I, Ionita, I, Schwarz, Jr., S, Veciana, J, Sala, S, Royo, M, Córdoba, A, Danino, D, Pedersen, J S, González-Mira, E, Abasolo, I & Ventosa, N 2021, ' Impact of Chemical Composition on the Nanostructure and Biological Activity of α-Galactosidase-Loaded Nanovesicles for Fabry Disease Treatment ', ACS applied materials & interfaces, vol. 13, no. 7, pp. 7825-7838 . https://doi.org/10.1021/acsami.0c16871
Digital.CSIC. Repositorio Institucional del CSIC
instname
Tomsen-Melero, J, Passemard, S, García-Aranda, N, Días-Riascos, Z V, González-Rioja, R, Pedersen, J N, Lyngsø, J, Merlo-Mas, J, Cristóbal-Lecina, E, Corchero, J L, Pulido, D, Cámara-Sánchez, P, Portnaya, I, Ionita, I, Schwarz, Jr., S, Veciana, J, Sala, S, Royo, M, Córdoba, A, Danino, D, Pedersen, J S, González-Mira, E, Abasolo, I & Ventosa, N 2021, ' Impact of Chemical Composition on the Nanostructure and Biological Activity of α-Galactosidase-Loaded Nanovesicles for Fabry Disease Treatment ', ACS applied materials & interfaces, vol. 13, no. 7, pp. 7825-7838 . https://doi.org/10.1021/acsami.0c16871
Digital.CSIC. Repositorio Institucional del CSIC
instname
Fabry disease is a rare lysosomal storage disorder characterized by a deficiency of α-galactosidase A (GLA), a lysosomal hydrolase. The enzyme replacement therapy administering naked GLA shows several drawbacks including poor biodistribution, limite