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Autor:
Adachi T; Department of Dermatology, Keio University School of Medicine, Tokyo 160-8582, Japan.; Department of Medical Regulatory Science, Graduate School of Medical Science, Kyoto Prefectural University of Medicine, Kyoto 602-8566, Japan.; United Japanese-Researchers Around-the-World (UJA), Isehara 259-1143, Japan., El-Hattab AW; Department of Clinical Sciences, College of Medicine, University of Sharjah, Sharjah 27272, United Arab Emirates.; MENA (Middle East and North Africa) Organization for Rare Diseases, Dubai 500767, United Arab Emirates.; Department of Pediatrics, University Hospital Sharjah, Sharjah 72772, United Arab Emirates., Jain R; Dystrophic Epidermolysis Bullosa Research Association (DEBRA), Singapore 059811, Singapore.; Asia Pacific Alliance of Rare Disease Organizations (APARDO), Singapore 188976, Singapore.; Language and Communication Centre, School of Humanities and Social Sciences, Nanyang Technological University, Singapore 639798, Singapore., Nogales Crespo KA; Policy Wisdom LLC, Quebradillas 00678-2705, Puerto Rico., Quirland Lazo CI; Health Technology Assessment Unit, Cancer Research Department, Arturo López Perez Foundation, Santiago 7500921, Chile.; School of Medicine, Universitat Autònoma de Barcelona, 080193 Barcelona, Spain.; Faculty of Pharmaceutical and Chemical Sciences, University of Chile, Santiago 8380000, Chile., Scarpa M; European Reference Network for Hereditary Metabolic Diseases (MetabERN), 33100 Udine, Italy.; Regional Coordinating Center for Rare Diseases Friuli Venezia Giulia, Udine University Hospital, 33100 Udine, Italy.; Brains for Brain Foundation, 35128 Padova, Italy., Summar M; The Translational Science Training Program, National Institutes of Health (NIH), Maryland, MD 20814, USA.; Children's National Medical Centre, Washington, DC 20010, USA.; National Organization for Rare Disorders (NORD), Quincy, MA 02169, USA.; Children's National Rare Disease Institute, Washington, DC 20012, USA.; Department of Pediatrics, George Washington University, Washington, DC 20052, USA., Wattanasirichaigoon D; Thai Rare Disease Foundation (ThaiRDF), Bangkok 10230, Thailand.; Prader-Willi Syndrome Association (PWSA) of Thailand, Department of Pediatrics, Faculty of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok 10400, Thailand.; Rare Disease Working Committee, Thai National Health Security Office (NHSO), Bangkok 10210, Thailand.; Sub-Working Committee for Rare Disease Medicine, Thailand National List of Essential Medicines (NLEM), National Drug Policy Division, Food and Drug Administration, Nonthaburi 11000, Thailand.; Medical Genetics Network, Genetics Society of Thailand, Bangkok 10330, Thailand.; Thailand Medical Genetics and Genomics Association (TMGGA), Bangkok 10510, Thailand.; Asia Pacific Society of Human Genetics (APSHG), Singapore 229899, Singapore.; Department of Pediatrics, Faculty of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok 10400, Thailand.
Publikováno v:
International journal of environmental research and public health [Int J Environ Res Public Health] 2023 Mar 08; Vol. 20 (6). Date of Electronic Publication: 2023 Mar 08.