Zobrazeno 1 - 2
of 2
pro vyhledávání: '"Preston N. Samowitz"'
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 19, Iss , Pp 474-485 (2020)
No treatment is available to address the unmet needs of mucopolysaccharidosis (MPS) IIIA patients. Targeting the root cause, we developed a new self-complementary adeno-associated virus 9 (scAAV9) vector to deliver the human N-sulfoglucosamine sulfoh
Externí odkaz:
https://doaj.org/article/c5adf3fe47a8472e979b7018ac52acca
Autor:
Tierra A. Bobo, Preston N. Samowitz, Michael I. Robinson, Laura I. Montes, Lawrence J. Forsberg, Richard Feng, Nathan I. Nicely, Haiyan Fu
Publikováno v:
Gene Therapy. 30:377-385
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::332acd01a0af1e78c538f7a33610846b
https://doi.org/10.1038/s41434-022-00368-9
https://doi.org/10.1038/s41434-022-00368-9