Development of a Gene Therapy Vector for RDH12 -Associated Retinal Dystrophy.

Autor: Feathers KL; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan., Jia L; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan., Perera ND; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan., Chen A; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan., Presswalla FK; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan., Khan NW; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan., Fahim AT; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan., Smith AJ; Department of Genetics, University College London Institute of Ophthalmology, London, United Kingdom., Ali RR; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan.; Department of Genetics, University College London Institute of Ophthalmology, London, United Kingdom., Thompson DA; Department of Ophthalmology and Visual Sciences, University of Michigan Medical School, Ann Arbor, Michigan.; Department of Biological Chemistry, University of Michigan Medical School, Ann Arbor, Michigan.

Publikováno v: Human gene therapy [Hum Gene Ther] 2019 Nov; Vol. 30 (11), pp. 1325-1335. Date of Electronic Publication: 2019 Aug 05.