Zobrazeno 1 - 10
of 120
pro vyhledávání: '"Philippe Veron"'
Autor:
Ai Vu Hong, Laurence Suel, Eva Petat, Auriane Dubois, Pierre-Romain Le Brun, Nicolas Guerchet, Philippe Veron, Jérôme Poupiot, Isabelle Richard
Publikováno v:
Nature Communications, Vol 15, Iss 1, Pp 1-20 (2024)
Abstract Current adeno-associated virus (AAV) gene therapy using nature-derived AAVs is limited by non-optimal tissue targeting. In the treatment of muscular diseases (MD), high doses are often required but can lead to severe adverse effects. Here, w
Externí odkaz:
https://doaj.org/article/2e8bc0e4254344a1a716b976440ae501
Autor:
Rita Ferla, Fabio Dell’Aquila, Monica Doria, Maria Ferraiuolo, Alessia Noto, Fabiana Grazioli, Virginia Ammendola, Francesco Testa, Paolo Melillo, Carolina Iodice, Giulia Risca, Novella Tedesco, Pierre Romain le Brun, Enrico Maria Surace, Francesca Simonelli, Stefania Galimberti, Maria Grazia Valsecchi, Jean-Brice Marteau, Philippe Veron, Stefano Colloca, Alberto Auricchio
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 28, Iss , Pp 396-411 (2023)
Gene therapy of Usher syndrome type 1B (USH1B) due to mutations in the large Myosin VIIA (MYO7A) gene is limited by the packaging capacity of adeno-associated viral (AAV) vectors. To overcome this, we have previously developed dual AAV8 vectors which
Externí odkaz:
https://doaj.org/article/61581d1038c94d21b99808688a92c247
Publikováno v:
Disegnare con, Vol 14, Iss 26, Pp 1-13 (2021)
In recent decades, cultural heritage survey practices have significantly evolved due to the increasing use of digitization tools providing quick and easy access to faithful copies of study objects. While these digital data have clear advantages, espe
Externí odkaz:
https://doaj.org/article/c8d1ceaa974f4eb7b6a5f6a857aa151d
Publikováno v:
Remote Sensing, Vol 15, Iss 9, p 2408 (2023)
In the field of digital cultural heritage (DCH), 2D/3D digitization strategies are becoming more and more complex. The emerging trend of multimodal imaging (i.e., data acquisition campaigns aiming to put in cooperation multi-sensor, multi-scale, mult
Externí odkaz:
https://doaj.org/article/d235bd2d9d824649b5d1e76bbf5c1b8d
Autor:
Fanny Collaud, Giulia Bortolussi, Laurence Guianvarc’h, Sem J. Aronson, Thierry Bordet, Philippe Veron, Severine Charles, Patrice Vidal, Marcelo Simon Sola, Stephanie Rundwasser, Delphine G. Dufour, Florence Lacoste, Cyril Luc, Laetitia v. Wittenberghe, Samia Martin, Christine Le Bec, Piter J. Bosma, Andres F. Muro, Giuseppe Ronzitti, Matthias Hebben, Federico Mingozzi
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 12, Iss , Pp 157-174 (2019)
Adeno-associated viruses (AAVs) are among the most efficient vectors for liver gene therapy. Results obtained in the first hemophilia clinical trials demonstrated the long-term efficacy of this approach in humans, showing efficient targeting of hepat
Externí odkaz:
https://doaj.org/article/721441a735dc4663ac629a4a43fbb03b
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy
Autor:
Caroline Le Guiner, Laurent Servais, Marie Montus, Thibaut Larcher, Bodvaël Fraysse, Sophie Moullec, Marine Allais, Virginie François, Maeva Dutilleul, Alberto Malerba, Taeyoung Koo, Jean-Laurent Thibaut, Béatrice Matot, Marie Devaux, Johanne Le Duff, Jack-Yves Deschamps, Inès Barthelemy, Stéphane Blot, Isabelle Testault, Karim Wahbi, Stéphane Ederhy, Samia Martin, Philippe Veron, Christophe Georger, Takis Athanasopoulos, Carole Masurier, Federico Mingozzi, Pierre Carlier, Bernard Gjata, Jean-Yves Hogrel, Oumeya Adjali, Fulvio Mavilio, Thomas Voit, Philippe Moullier, George Dickson
Publikováno v:
Nature Communications, Vol 8, Iss 1, Pp 1-15 (2017)
Duchenne muscular dystrophy is a progressive degenerative disease of muscles caused by mutations in the dystrophin gene. Here the authors use AAV vectors to deliver microdystrophin to dogs with muscular dystrophy, and show restoration of dystrophin e
Externí odkaz:
https://doaj.org/article/d425f7f6bf364aa99c6850ae61ecdd6b
Autor:
Elena Piletska, Philippe Veron, Bérangère Bertin, Federico Mingozzi, Donald Jones, Joseph Earley, Kal Karim, Alvaro GARCIA CRUZ, Sergey A. Piletsky
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::a758c2a414ec993dd0b693a05a750a01
https://doi.org/10.2139/ssrn.4352168
https://doi.org/10.2139/ssrn.4352168
Publikováno v:
Computers in Industry
Computers in Industry, Elsevier, 2021, 132, pp.103527. ⟨10.1016/j.compind.2021.103527⟩
Computers in Industry, Elsevier, 2021, 132, pp.103527. ⟨10.1016/j.compind.2021.103527⟩
International audience; Manufacturing industry needs access to the data in order to realise its activities but also to generate new value-added knowledge. Nevertheless, it is confronted with a large and growing volume of heterogeneous data which limi
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2128bc7aa5707fa56e1cf3b5c7a59a1e
https://hdl.handle.net/10985/20716
https://hdl.handle.net/10985/20716
Publikováno v:
Remote Sensing, Vol 12, Iss 12, p 2051 (2020)
Imaging techniques and Image Based-Modeling (IBM) practices in the field of Cultural Heritage (CH) studies are nowadays no longer used as one-shot applications but as various and complex scenarios involving multiple modalities; sensors, scales, spect
Externí odkaz:
https://doaj.org/article/06ca0c2c71fb4e4293a458a67c3ae28b
Autor:
Nicola Brunetti-Pierri, Rita Ferla, Virginia Maria Ginocchio, Alessandro Rossi, Simona Fecarotta, Roberta Romano, Giancarlo Parenti, Yilmaz Yildiz, Stefano Zancan, Valentina Pecorella, Margherita Dell’Anno, Mafalda Graziano, Marialuisa Alliegro, Generoso Andria, Francesca Santamaria, Raffaella Brunetti-Pierri, Francesca Simonelli, Vincenzo Nigro, Maria Vargas, Giuseppe Servillo, Francesco Borgia, Ernesto Soscia, Marco Gargaro, Silvia Funghini, Novella Tedesco, Pierre Romain Le Brun, Charles A. Rupar, Chitra Prasad, Mar O’Callaghan, John J. Mitchell, Olivier Danos, Jean-Brice Marteau, Stefania Galimberti, Maria Grazia Valsecchi, Philippe Veron, Federico Mingozzi, Francesca Fallarino, Giancarlo la Marca, H. Serap Sivri, Alberto Auricchio
Publikováno v:
NEJM Evidence. 1
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::93d416c60dd7074db1fccb900afbb5ac
https://doi.org/10.1056/evidoa2200052
https://doi.org/10.1056/evidoa2200052