Liver-Directed Adeno-Associated Virus–Mediated Gene Therapy for Mucopolysaccharidosis Type VI

Autor: Nicola Brunetti-Pierri, M. D. 1 2, Rita Ferla, Ph. D. 1, 2, Virginia Maria Ginocchio, M. D., Alessandro Rossi, Ph. D. 2, Simona Fecarotta, Ph. D. 3, Roberta Romano, M. D. 2, Giancarlo Parenti, Yilmaz Yildiz, Ph. D. 4, Stefano Zancan, M. Sc. 5, Valentina Pecorella, M. Sc. 1, Margherita Dell’Anno, Mafalda Graziano, Marialuisa Alliegro, Generoso Andria, Francesca Santamaria, Raffaella Brunetti-Pierri, Ph. D. 6, Francesca Simonelli, M. D. 6, Vincenzo Nigro, M. D. 1 7, Maria Vargas, M. D. 8, Giuseppe Servillo, Francesco Borgia, M. D. 9, Ernesto Soscia, M. D. 10, Marco Gargaro, Ph. D. 11, Silvia Funghini, Ph. D. 12, Novella Tedesco, M. Sc. 13, Pierre Romain Le Brun, Charles A. Rupar, Ph. D., F. C. C. M. G. 15, Chitra Prasad, M. D. F. R. C. P., Mar O’Callaghan, Ph. D. 16, John J. Mitchell, F. R. C. P. 17, Olivier Danos, Ph. D. 19, Jean-Brice Marteau, Ph. D. 20, Stefania Galimberti, Ph. D. 21, Maria Grazia Valsecchi, Philippe Veron, Ph. D. 13, Federico Mingozzi, Francesca Fallarino, Giancarlo la Marca, Pharm. Sc. 12, H. Serap Sivri, M. D. 4, and Alberto Auricchio, M. D. 1

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=od______3730::5738f09a90c8a5d20b8239b9aff172c3
https://hdl.handle.net/11588/912900