Profile of lumacaftor/ivacaftor combination: potential in the treatment of cystic fibrosis

Autor: Arends AM, Pettit RS

Publikováno v: Orphan Drugs: Research and Reviews, Vol 2015, Iss Issue 1, Pp 61-68 (2015)

Alexandria M Arends,1 Rebecca S Pettit2 1Department of Pharmacy, Indiana University Health, 2Department of Pharmacy, Riley Hospital for Children, Indianapolis, IN, USA Objective: To review the cystic fibrosis transmembrane conductance regulator (CFTR

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doajarticles::0d49835eed90bd52b04716899563955a
https://www.dovepress.com/profile-of-lumacaftorivacaftor-combination-potential-in-the-treatment--peer-reviewed-article-ODRR

Papilledema in Children With Cystic Fibrosis Receiving Elexacaftor/Tezacaftor/Ivacaftor: A Multicenter Case Series.

Autor: Kam CW; Department of Pharmacy, University of North Carolina Medical Center, Chapel Hill, North Carolina, USA., McKinzie CJ; Department of Pharmacy, University of North Carolina Medical Center, Chapel Hill, North Carolina, USA., Omecene NE; Department of Pharmacotherapy and Outcomes Science, Virginia Commonwealth University School of Pharmacy, Richmond, Virginia, USA., Peters S; College of Pharmacy and Allied Health Professions, South Dakota State University, Brookings, South Dakota, USA., Pettit RS; Department of Pharmacy, Riley Hospital for Children, Indiana University Health, Indianapolis, Indiana, USA., Poisson MO; Department of Pharmacy, Children's Hospital of Georgia, Augusta, Georgia, USA., Witte J; Department of Pharmacy, Driscoll Children's Hospital, Corpus Christi, Texas, USA.

Publikováno v: Pediatric pulmonology [Pediatr Pulmonol] 2024 Dec 20, pp. e27455. Date of Electronic Publication: 2024 Dec 20.

Elexacaftor/Tezacaftor/Ivacaftor use in Pediatric Cystic Fibrosis Patients with Advanced Liver Disease.

Autor: Protich HE; Department of Pharmacy, Riley Hospital for Children at IU Health, 705 Riley Hospital Drive, Simon Family Tower W6111, Indianapolis, IN, USA. Electronic address: hprotich@butler.edu., Molleston JP; Department of Pediatric Gastroenterology, Indiana University School of Medicine, 705 Riley Hospital Drive, Room 4210, Indianapolis, Indiana, USA., Bozic M; Department of Pediatric Gastroenterology, Indiana University School of Medicine, 705 Riley Hospital Drive, Room 4210, Indianapolis, Indiana, USA., Pettit RS; Department of Pharmacy, Riley Hospital for Children at IU Health, 705 Riley Hospital Drive, Simon Family Tower W6111, Indianapolis, IN, USA.

Publikováno v: Journal of cystic fibrosis : official journal of the European Cystic Fibrosis Society [J Cyst Fibros] 2024 Nov; Vol. 23 (6), pp. 1122-1128. Date of Electronic Publication: 2024 Apr 04.

Cystic fibrosis screening, evaluation, and management of hepatobiliary disease consensus recommendations.

Autor: Sellers ZM; Department of Pediatrics, Division of Pediatric Gastroenterology, Hepatology, and Nutrition, Stanford University, Palo Alto, California, USA., Assis DN; Department of Medicine, Section of Digestive Diseases, Yale School of Medicine, New Haven, Connecticut, USA., Paranjape SM; Division of Pediatric Pulmonology, Johns Hopkins University, Baltimore, Maryland, USA., Sathe M; Department of Pediatrics, Division of Pediatric Gastroenterology and Nutrition, UT Southwestern, Dallas, Texas, USA., Bodewes F; Department of Pediatric Gastroenterology, University Medical Center Groningen, Groningen, The Netherlands., Bowen M; Department of Advanced Lung Disease and Lung Transplant, Inova Fairfax Hospital, Falls Church, Virginia, USA., Cipolli M; Cystic Fibrosis Center, Azienda Ospedaliera Universitaria Integrata, Verona, Italy., Debray D; Pediatric Hepatology Unit, AP-HP, HôpitalNecker-Enfants malades, Paris, France., Green N; Department of Pediatrics, Division of Pediatric Gastroenterology, Hepatology, and Nutrition, Seattle Children's Hospital and University of Washington, Seattle, Washington State, USA., Hughan KS; Department of Pediatrics, Division of Pediatric Endocrinology and Metabolism, UPMC Children's Hospital of Pittsburgh and University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, USA., Hunt WR; Department of Medicine, Division of Pulmonary, Allergy, Critical Care and Sleep, Emory University, Atlanta, Georgia, USA., Leey J; Department of Medicine, Division of Endocrinology, Diabetes and Metabolism, University of Florida, Gainesville, Florida, USA., Ling SC; Department of Paediatrics, Division of Gastroenterology, Hepatology & Nutrition, The Hospital for Sick Children, University of Toronto, Toronto, Ontario, Canada., Morelli G; Department of Medicine, Division of Gastroenterology, Hepatology, and Nutrition, University of Florida, Gainesville, Florida, USA., Peckham D; Leeds Institute of Medical Research at St. James's, University of Leeds, Leeds, UK., Pettit RS; Riley Hospital for Children at IU Health, Indianapolis, Indiana, USA., Philbrick A; Department of Specialty Pharmacy, Northwestern Medicine, Chicago, Illinois, USA., Stoll J; Department of Pediatrics, Division of Gastroenterology, Hepatology, and Nutrition, Washington University School of Medicine, St Louis, Missouri, USA., Vavrina K; University of Texas, Health Science Center, San Antonio, Texas, USA., Allen S; CF Parent Community Advisor to Cystic Fibrosis Foundation, USA., Goodwin T; CF Parent Community Advisor to Cystic Fibrosis Foundation, USA., Hempstead SE; Cystic Fibrosis Foundation, Bethesda, Maryland, USA., Narkewicz MR; Department of Pediatrics, Section of Pediatric Gastroenterology, Hepatology, and Nutrition, Digestive Health Institute, Children's Hospital Colorado, University of Colorado School of, Aurora, Colorado, USA.

Publikováno v: Hepatology (Baltimore, Md.) [Hepatology] 2024 May 01; Vol. 79 (5), pp. 1220-1238. Date of Electronic Publication: 2023 Oct 26.

Educational Initiative to Increase Knowledge for Transition to Adult Care in Adolescents With Cystic Fibrosis.

Autor: Perez A; Global Medical Affairs (AP), Northeastern University, Boston, MA., Vogt H; Department of Pharmacy (HV), Indiana University Health, Indianapolis, IN., Pettit RS; Department of Pharmacy (RSP), Riley Hospital for Children at Indiana University Health, Indianapolis, IN.

Publikováno v: The journal of pediatric pharmacology and therapeutics : JPPT : the official journal of PPAG [J Pediatr Pharmacol Ther] 2023; Vol. 28 (8), pp. 741-746. Date of Electronic Publication: 2023 Dec 12.