Zobrazeno 1 - 4
of 4
pro vyhledávání: '"Pediatric Neuromuscular Clinical Research Network"'
Autor:
Dione T Kobayashi, Jing Shi, Laurie Stephen, Karri L Ballard, Ruth Dewey, James Mapes, Brett Chung, Kathleen McCarthy, Kathryn J Swoboda, Thomas O Crawford, Rebecca Li, Thomas Plasterer, Cynthia Joyce, Biomarkers for Spinal Muscular Atrophy Study Group, Wendy K Chung, Petra Kaufmann, Basil T Darras, Richard S Finkel, Douglas M Sproule, William B Martens, Michael P McDermott, Darryl C De Vivo, Pediatric Neuromuscular Clinical Research Network, Michael G Walker, Karen S Chen
Publikováno v:
PLoS ONE, Vol 8, Iss 4, p e60113 (2013)
OBJECTIVESSpinal Muscular Atrophy (SMA) presents challenges in (i) monitoring disease activity and predicting progression, (ii) designing trials that allow rapid assessment of candidate therapies, and (iii) understanding molecular causes and conseque
Externí odkaz:
https://doaj.org/article/bde3060c6f104867b0d25e27fac0f7ae
Autor:
Kaufmann, P., Kang, P.B., Gooch, C.L., McDermott, M.P., Darras, B.T., Finkel, R.S., Yang, M.L., Sproule, D.M., Chung, W.K., De Vivo, D.C., M.S.G. Pediatric Neuromuscular Clinical Research Network
Publikováno v:
In Clinical Neurophysiology June 2014 125 Supplement 1:S198-S198
Autor:
Glanzman AM, McDermott MP, Montes J, Martens WB, Flickinger J, Riley S, Quigley J, Dunaway S, O'Hagen J, Deng L, Chung WK, Tawil R, Darras BT, Yang M, Sproule D, De Vivo DC, Kaufmann P, Finkel RS;, Pediatric Neuromuscular Clinical Research Network for Spinal Muscular Atrophy (PNCR);, Muscle Study Group (MSG).
Publikováno v:
Pediatric Physical Therapy; 2011 Winter, Vol. 23 Issue 4, p322-326, 5p
Autor:
Montes J, McDermott MP, Martens WB, Dunaway S, Glanzman AM, Riley S, Quigley J, Montgomery MJ, Sproule D, Tawil R, Chung WK, Darras BT, De Vivo DC, Kaufmann P, Finkel RS, Muscle Study Group and the Pediatric Neuromuscular Clinical Research Network, Montes, J, McDermott, M P, Martens, W B, Dunaway, S
Publikováno v:
Neurology; 3/9/2010, Vol. 74 Issue 10, p833-838, 6p