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pro vyhledávání: '"Pamela Appleton"'
Autor:
Sathyajith Buddhika Ambawatte, Derek Weidner, Sherryl Chatfield, Pamela Appleton, Emma Matthews, Niranjanan Nirmalananthan, Clare Galtrey
Publikováno v:
Journal of Neurology, Neurosurgery & Psychiatry. 93:e2.152
Risdiplam is a pre-mRNA splicing modifier designed to treat 5q-SMA. We describe our experience prescrib- ing Risdiplam to adults with type-2 SMA with a wider range of ages and comorbidities than in clinical trials.Risdiplam was prescribed for nine pe
Autor:
Sathyajith Buddhika Ambawatte, Sahil Chhabda, Declan Johnson, Derek Weidner, Sherryl Chatfield, Pamela Appleton, Emma Matthews, Niranjanan Nirmalananthan, Clare Galtrey
Publikováno v:
Journal of Neurology, Neurosurgery & Psychiatry. 93:e2.151
We describe nusinersen, the only licensed treatment for adults with SMA in the UK, administra- tion with Single-Plane-Fluoroscopic-Guided(SPFG), Bi-Plane-Fluoroscopic-Guided(BPFG), or Computerised-Tomography-guided(CTG).We treated three patients with