Gene Therapy for Spinal Muscular Atrophy (SMA): A Review of Current Challenges and Safety Considerations for Onasemnogene Abeparvovec (Zolgensma).

Autor: Ogbonmide T; College of Medicine, Saint James School of Medicine, Saint Vincent and Grenadines, VCT., Rathore R; Pharmacology and Therapeutics, Saint James School of Medicine, Saint Vincent and grenadines, VCT., Rangrej SB; Anatomy/Research, Saint James School of Medicine, Saint Vincent and Grenadines, VCT., Hutchinson S; Pharmacology, Saint James School of Medicine, Saint Vincent and Grenadines, VCT., Lewis M; College of Medicine, Saint James School of Medicine, Saint Vincent and Grenadines, VCT., Ojilere S; College of Medicine, Saint James School of Medicine, Saint Vincent and Grenadines, VCT., Carvalho V; College of Medicine, Saint James School of Medicine, Saint Vincent and Grenadines, VCT., Kelly I; Neurology, Saint James School of Medicine, Saint Vincent and Grenadines, VCT.

Publikováno v: Cureus [Cureus] 2023 Mar 15; Vol. 15 (3), pp. e36197. Date of Electronic Publication: 2023 Mar 15 (Print Publication: 2023).