Zobrazeno 1 - 2
of 2
pro vyhledávání: '"Muhammad Ameer Saif"'
Autor:
Muhammad Ameer Saif, Brian W. Bigger, Karen E Brookes, Jean Mercer, Karen L. Tylee, Heather J. Church, Denise K. Bonney, Simon Jones, J. Ed Wraith, Robert F. Wynn
Publikováno v:
Haematologica, Vol 97, Iss 9 (2012)
Background Mucopolysaccharidosis type I is caused by deficiency of α-L-iduronidase. Currently available treatment options include an allogeneic hematopoietic stem cell transplant and enzyme replacement therapy. Exogenous enzyme therapy appears promi
Externí odkaz:
https://doaj.org/article/4b0beb106a904a08bfa43632996ccc6a
Autor:
Sujith Samarasinghe, Nick Goulden, Steve Keogh, Colin G. Steward, Philip Connor, Maria Pelidis, Persis Amrolia, Rod Skinner, Mathew Stubbs, Muhammad Ameer Saif, Amrana Qureshi, Sarah Lawson, Rachael Hough, Kanchan Rao, Peter Carey, Denise Bonney, Ajay Vora, David Webb, Graham Stewart, Rob Wynn, Alice Norton, Brenda Gibson, Prashant Hiwarkar, Paul Veys, Stefan Meyer
Publikováno v:
British journal of haematology. 157(3)
Summary We retrospectively analysed the outcome of consecutive children with idiopathic severe aplastic anaemia in the United Kingdom who received immunosuppressive therapy (IST) or matched unrelated donor (MUD) haematopoietic stem cell transplantati