Gene Therapy for Inherited Liver Disease: To Add or to Edit.

Autor: Chen, Yue¹ (AUTHOR) y.chen2@amsterdamumc.nl, van Til, Niek P.^2,3 (AUTHOR) n.p.vantil@amsterdamumc.nl, Bosma, Piter J.¹ (AUTHOR) p.j.bosma@amsterdamumc.nl

Publikováno v: International Journal of Molecular Sciences. Dec2024, Vol. 25 Issue 23, p12514. 19p.

A prospective survey of Streptococcus pyogenes infections in French Brittany from 2009 to 2017: Comprehensive dynamic of new emergent emm genotypes.

Autor: Boukthir S; CHU de Rennes, Service de Bactériologie-Hygiène Hospitalière, Rennes, France.; Inserm, CIC 1414, Rennes, France.; Université Rennes 1, Faculté de Médecine, Rennes, France., Moullec S; Inserm, CIC 1414, Rennes, France.; Université Rennes 1, Faculté de Médecine, Rennes, France., Cariou ME; Centre Hospitalier de 'Bretagne Sud', Laboratoire de Biologie, Lorient, France., Meygret A; CHU de Rennes, Service de Bactériologie-Hygiène Hospitalière, Rennes, France.; Université Rennes 1, Faculté de Médecine, Rennes, France., Morcet J; CHU de Rennes, Service de Bactériologie-Hygiène Hospitalière, Rennes, France.; Inserm, CIC 1414, Rennes, France., Faili A; Inserm, CIC 1414, Rennes, France.; Université Rennes 1, Faculté de Pharmacie, Rennes, France., Kayal S; CHU de Rennes, Service de Bactériologie-Hygiène Hospitalière, Rennes, France.; Inserm, CIC 1414, Rennes, France.; Université Rennes 1, Faculté de Médecine, Rennes, France.

Publikováno v: PloS one [PLoS One] 2020 Dec 17; Vol. 15 (12), pp. e0244063. Date of Electronic Publication: 2020 Dec 17 (Print Publication: 2020).

Capsid-specific removal of circulating antibodies to adeno-associated virus vectors.

Autor: Bertin B; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Veron P; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Leborgne C; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Deschamps JY; Atlantic Gene Therapies, Centre de Boisbonne, ONIRIS, La Chantrerie, BP 40706, 44307, Nantes, France., Moullec S; Atlantic Gene Therapies, Centre de Boisbonne, ONIRIS, La Chantrerie, BP 40706, 44307, Nantes, France., Fromes Y; Institute of Myology, Sorbonne University and INSERM U974, 105 boulevard de l'Hopital, 75013, Paris, France., Collaud F; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Boutin S; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Latournerie V; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., van Wittenberghe L; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Delache B; CEA, Université Paris-Sud 11, INSERM U1184, Immunology of Viral Infections and Autoimmune Diseases, IDMIT Department, IBFJ, Fontenay-aux-Roses, 92265, France., Le Grand R; CEA, Université Paris-Sud 11, INSERM U1184, Immunology of Viral Infections and Autoimmune Diseases, IDMIT Department, IBFJ, Fontenay-aux-Roses, 92265, France., Dereuddre-Bosquet N; CEA, Université Paris-Sud 11, INSERM U1184, Immunology of Viral Infections and Autoimmune Diseases, IDMIT Department, IBFJ, Fontenay-aux-Roses, 92265, France., Benveniste O; Institute of Myology, Sorbonne University and INSERM U974, 105 boulevard de l'Hopital, 75013, Paris, France.; Assistance Publique-Hôpitaux de Paris, 75013, Paris, France., Moullier P; Atlantic Gene Therapies, Centre de Boisbonne, ONIRIS, La Chantrerie, BP 40706, 44307, Nantes, France., Masurier C; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Merten O; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France., Mingozzi F; Genethon and INSERM U951, 1 rue de l'internationale, 91000, Evry, France. fmingozzi@genethon.fr.

Publikováno v: Scientific reports [Sci Rep] 2020 Jan 21; Vol. 10 (1), pp. 864. Date of Electronic Publication: 2020 Jan 21.

Quantitative evaluation of locoregional high venous pressure rAAV8-U7-ESE6-ESE8 exon-skipping therapy in the GRMD dog using NMR H-1 imaging and P-31 spectroscopy

Autor: Thibaud, J. L., Wary, C., Moullec, S., Azzabou, N., Le Guiner, C., Garcia, L., Montus, M., Cherel, Yan, Fromes, Y., Servais, L., Roques, S., Moullier, P., Voit, T., Carlier, P. G.

Publikováno v: Neuromuscular Disorders
17. International Congress of the World Muscle Society
17. International Congress of the World Muscle Society, Oct 2012, Perth, Australia. ⟨10.1016/j.nmd.2012.06.188⟩

International audience

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::4016846386ff4ea7338f94290161a233
https://hal.inrae.fr/hal-02749400

Recent Advances in Gene Therapy for Hemophilia: Projecting the Perspectives.

Autor: Chernyi, Nikita¹ (AUTHOR), Gavrilova, Darina² (AUTHOR), Saruhanyan, Mane¹ (AUTHOR), Oloruntimehin, Ezekiel S.¹ (AUTHOR), Karabelsky, Alexander³ (AUTHOR), Bezsonov, Evgeny^1,2 (AUTHOR) bezsonov_e_e@staff.sechenov.ru, Malogolovkin, Alexander^1,3 (AUTHOR) bezsonov_e_e@staff.sechenov.ru

Publikováno v: Biomolecules (2218-273X). Jul2024, Vol. 14 Issue 7, p854. 27p.