NEW THERAPEUTIC APPROACHES AND THEIR READOUT: O.16Myostatin expression is a reliable and quantifiable biomarker to monitor dose-dependent drug response in muscular dystrophy

Autor: Dumonceaux, J., Mariot, V., Le Guiner, C., Barthelemy, I., Hourdé, C., Montus, M., Blot, S., Voit, T.

Publikováno v: In Neuromuscular Disorders October 2018 28 Supplement 2:S91-S91

S05 - Myostatin expression in neuromuscular diseases

Autor: Mariot, V., Le Guiner, C., Inès, B., Hourdé, C., Montus, M., Blot, S., Voit, T., Dumonceaux, J.

Publikováno v: In Neuromuscular Disorders April 2018 28 Supplement 1:S2-S2

Dystrophin rescue needed to recover a correct location of nNOS and the return to a normalized RyR1 status in treated GRMD dogs

Autor: Gentil, C., Le Guiner, C., Cherel, Yan, Montus, M., Moulier, P., Servais, L., Voit, T., Pietri-Rouxel, F.

Publikováno v: Neuromuscular Disorders
18. International Congress of The World Muscle Society
18. International Congress of The World Muscle Society, Oct 2013, Asilomar, California, United States. ⟨10.1016/j.nmd.2013.06.701⟩

International audience

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::cfbfce301cff7ca99e5ad3e5676f5d4e
https://hal.inrae.fr/hal-02747723

Quantitative NMR 1H imaging and 31P spectroscopy evaluation of locoregional high venous pressure rAAV8-U7-ESE6-ESE8 exon-skipping therapy in the GRMD

Autor: Thibaud, J. L., Wary, C., Moullec, S., Azzabou, N., Le Guiner, C., Garcia, L., Montus, M., Cherel, Yan, Fromes, Y., Servais, L., Roques, S., Moullier, P., Voit, T., Carlier, P. G.

Publikováno v: Human Gene Therapy
European Society of Gene and Cell Therapy/French Society of Cell and Gene Therapy Collaborative Congress
European Society of Gene and Cell Therapy/French Society of Cell and Gene Therapy Collaborative Congress, Oct 2012, Versailles, France

National audience

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::be6ef709f4a1c316ce06bb8703241000
https://hal.inrae.fr/hal-02747019

Progress towards sytemic delivery of AAV-based dystrophin gene correction

Autor: Voit, T., Servais, L., Montus, M., Fromes, Y., Cherel, Yan, Le Guiner, C., Garcia, L., Hogrel, J.Y., Carlier, P., Moullier, P.

Publikováno v: TREAT-NMD International conference
TREAT-NMD International conference, Nov 2011, Genève, Switzerland. n.p

International audience

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::a72bebf87806ca97cf2c81adda7cf137
https://hal.inrae.fr/hal-02805630