AAV-Mediated CRISPR/Cas9 Gene Editing in Murine Phenylketonuria

Autor: Richards, Daelyn Y., Winn, Shelley R., Dudley, Sandra, Nygaard, Sean, Mighell, Taylor L., Grompe, Markus, Harding, Cary O.

Publikováno v: In Molecular Therapy - Methods & Clinical Development 12 June 2020 17:234-245

A Saturation Mutagenesis Approach to Understanding PTEN Lipid Phosphatase Activity and Genotype-Phenotype Relationships

Autor: Mighell, Taylor L., Evans-Dutson, Sara, O’Roak, Brian J.

Publikováno v: In The American Journal of Human Genetics 3 May 2018 102(5):943-955

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AAV-Mediated CRISPR/Cas9 Gene Editing in Murine Phenylketonuria.

Autor: Richards DY; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, OR 97239, USA., Winn SR; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, OR 97239, USA., Dudley S; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, OR 97239, USA., Nygaard S; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, OR 97239, USA., Mighell TL; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, OR 97239, USA., Grompe M; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, OR 97239, USA., Harding CO; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, OR 97239, USA.; Department of Pediatrics, Oregon Health & Science University, Portland, OR 97239, USA.

Publikováno v: Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2019 Dec 24; Vol. 17, pp. 234-245. Date of Electronic Publication: 2019 Dec 24 (Print Publication: 2020).