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pro vyhledávání: '"Meghan Crone"'
Autor:
Laura McAdam, James J. Dowling, Monique Taillon, Anna McCormick, Said M’dahoma, Gerald Pfeffer, Cam-Tu Emilie Nguyen, Colleen O'Connell, Craig Campbell, Scott Worley, Hernan Gonorazky, Alex MacKenzie, Aaron Izenberg, Jiri Vajsar, Peter Dobrowolski, Emily Butler, Jean K. Mah, Simona Hasal, Alier Marerro, Hugh J. McMillan, Garth Smith, Erin K. O'Ferrall, Hanns Lochmüller, Michelle M. Mezei, Christen Shoesmith, Nicolas Dupré, Victoria Hodgkinson, Nicolas Chrestian, Louise R. Simard, Meghan Crone, Cecile Phan, Jodi Warman Chardon, Xavier Rodrigue, Jordan Sheriko, Michel Melanson, Kathy Selby, Angela Genge, Edward Leung, Maryam Oskoui, Kristine M. Chapman, Stephanie Plamondon, Kerri Schellenberg, Rami Massie, Bernard Brais, Joshua J. Lounsberry, Susan Dojeiji, Sean W. Taylor, Wendy Johnston, Chantal Poulin, Lawrence Korngut
Publikováno v:
Paediatrics Publications
The Canadian Journal of Neurological Sciences. Le Journal Canadien Des Sciences Neurologiques
The Canadian Journal of Neurological Sciences. Le Journal Canadien Des Sciences Neurologiques
Background:Spinal muscular atrophy (SMA) is a devastating rare disease that affects individuals regardless of ethnicity, gender, and age. The first-approved disease-modifying therapy for SMA, nusinursen, was approved by Health Canada, as well as by A