Výsledky vyhledávání - "Maureen T. McBride"

Results at 2 Years after Gene Therapy for RPE65-Deficient Leber Congenital Amaurosis and Severe Early-Childhood-Onset Retinal Dystrophy

Autor: Roberto Calcedo, Laura R Erker, William W. Hauswirth, Jeffrey D. Chulay, Margaret Humphries, Mark E. Pennesi, Lauren Jensen, David J. Wilson, J. Timothy Stout, Terence R. Flotte, Richard G. Weleber, Maureen T. McBride, Shalesh Kaushal

Publikováno v: Ophthalmology. 123(7)

Purpose To provide an initial assessment of the safety of a recombinant adeno-associated virus vector expressing RPE65 (rAAV2-CB-hRPE65) in adults and children with retinal degeneration caused by RPE65 mutations. Design Nonrandomized, multicenter cli

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::35a83139e2ae8405cdc7d24026085973
https://pubmed.ncbi.nlm.nih.gov/27102010

Zobrazit plný text záznamu

Vyhledávací nástroje:

Upřesnit hledání