Zobrazeno 1 - 3
of 3
pro vyhledávání: '"Marti DiPietro"'
Autor:
Liron Elkouby, Sean M. Armour, Raffaella Toso, Marti DiPietro, Robert J. Davidson, Giang N. Nguyen, Mallory Willet, Stephanie Kutza, Joseph Silverberg, Jennifer Frick, Marco Crosariol, Yuhuan Wang, Chuansong Wang, Katherine A. High, Denise E. Sabatino, Xavier M. Anguela
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 24, Iss , Pp 20-29 (2022)
Extensive clinical data from liver-mediated gene therapy trials have shown that dose-dependent immune responses against the vector capsid may impair or even preclude transgene expression if not managed successfully with prompt immune suppression. The
Externí odkaz:
https://doaj.org/article/8d15f9b5838e44d49c75621a886fa6f5
Autor:
Lizbeth M. Hoos, Laura Sepp-Lorenzino, Walter Strapps, John Levorse, Dietmar Seiffert, Karen R. Leander, Marti DiPietro, Yuchen Zhou, Anil Thankappan, Weizhen Wu, Tian-Quan Cai, Zuo Zhang, Zhu Chen, Yiming Xu, Marija Tadin-Strapps, Myung K. Shin, Patrick Andre, Joseph M. Metzger, Kunal Desai, KehDih Lai, Nina Jochnowitz, Ross Bentley
Publikováno v:
Thrombosis and haemostasis. 113(6)
SummaryHaemophilia A and B are characterised by a life-long bleeding predisposition, and several lines of evidence suggest that risks of atherothrombotic events may also be reduced. Establishing a direct correlation between coagulation factor levels,
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c451ee47e663a79cf3f2011d6a5ea178
https://pubmed.ncbi.nlm.nih.gov/25790442
https://pubmed.ncbi.nlm.nih.gov/25790442
Autor:
Xavier M. Anguela, Liron Elkouby, Marti DiPietro, Katherine A. High, Raffaella Toso, Robert J. Davidson, Denise E. Sabatino
Publikováno v:
Blood. 126:199-199
Clinical studies of adeno-associated viral (AAV)-mediated gene transfer of factor IX for hemophilia B have demonstrated long term expression of therapeutic levels of factor IX but revealed that the AAV vector dose may be limiting due to anti-AAV immu
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::89e7af0000963c742c359efc12347f0e
https://doi.org/10.1182/blood.v126.23.199.199
https://doi.org/10.1182/blood.v126.23.199.199