Zobrazeno 1 - 6
of 6
pro vyhledávání: '"Marta, Zinicola"'
Autor:
Rajeev Rai, Marianna Romito, Elizabeth Rivers, Giandomenico Turchiano, Georges Blattner, Winston Vetharoy, Dariusz Ladon, Geoffroy Andrieux, Fang Zhang, Marta Zinicola, Diego Leon-Rico, Giorgia Santilli, Adrian J. Thrasher, Alessia Cavazza
Publikováno v:
Nature Communications, Vol 11, Iss 1, Pp 1-15 (2020)
In recent years, hematopoietic stem cells gene editing has emerged as a promising tool to treat blood disorders. Here the authors develop a CRISPR/Cas9-based genome editing strategy that allows the precise correction of Wiskott-Aldrich Syndrome in vi
Externí odkaz:
https://doaj.org/article/e93094c9c51f4c1aa746e611fd6ea64c
Autor:
Constandinos Carserides, Kieron Smith, Marta Zinicola, Abhinav Kumar, Magda Swedrowska, Carlo Scala, Gary Cameron, Zoe Riches, Francesco Iannelli, Gianni Pozzi, Georgina L. Hold, Ben Forbes, Charles Kelly, Karolin Hijazi
Publikováno v:
Pharmaceutics, Vol 14, Iss 9, p 1938 (2022)
Modulation of drug transporter activity at mucosal sites of HIV-1 transmission may be exploited to optimize retention of therapeutic antiretroviral drug concentrations at target submucosal CD4+ T cells. Previously, we showed that darunavir was a subs
Externí odkaz:
https://doaj.org/article/ddf5f56e7556446f8f22c858e7c7072e
Autor:
William, Rae, John M, Sowerby, Dorit, Verhoeven, Mariam, Youssef, Prasanti, Kotagiri, Natalia, Savinykh, Eve L, Coomber, Alexis, Boneparth, Angela, Chan, Chun, Gong, Machiel H, Jansen, Romy, du Long, Giorgia, Santilli, Ilenia, Simeoni, Jonathan, Stephens, Kejia, Wu, Marta, Zinicola, Hana Lango, Allen, Helen, Baxendale, Dinakantha, Kumararatne, Effrossyni, Gkrania-Klotsas, Selma C, Scheffler Mendoza, Marco Antonio, Yamazaki-Nakashimada, Laura Berrón, Ruiz, Cesar Mauricio, Rojas-Maruri, Saul O, Lugo Reyes, Paul A, Lyons, Anthony P, Williams, Daniel J, Hodson, Gail A, Bishop, Adrian J, Thrasher, David C, Thomas, Michael P, Murphy, Timothy J, Vyse, Joshua D, Milner, Taco W, Kuijpers, Kenneth G C, Smith
Publikováno v:
Science immunology. 7(74)
Tumor necrosis factor receptor-associated factor 3 (TRAF3) is a central regulator of immunity. TRAF3 is often somatically mutated in B cell malignancies, but its role in human immunity is not defined. Here, in five unrelated families, we describe an
Autor:
Georges Blattner, Fang Zhang, Winston Vetharoy, Marianna Romito, Adrian J. Thrasher, Elizabeth Rivers, Dariusz Ladon, Marta Zinicola, Diego Leon-Rico, Rajeev Rai, Giandomenico Turchiano, Giorgia Santilli, Geoffroy Andrieux, Alessia Cavazza
Publikováno v:
Nature Communications, Vol 11, Iss 1, Pp 1-15 (2020)
Nature Communications
Nature Communications
Wiskott-Aldrich syndrome (WAS) is an X-linked primary immunodeficiency with severe platelet abnormalities and complex immunodeficiency. Although clinical gene therapy approaches using lentiviral vectors have produced encouraging results, full immune
Autor:
Adrian J. Thrasher, Simon Clare, Walmir Cutrim Aragão-Filho, Hubert B. Gaspar, Andrea Schejtman, Antonio Condino-Neto, Claire Booth, Giorgia Santilli, Siobhan O. Burns, Maren Weisser, Marta Zinicola, David C. Thomas
Publikováno v:
Gene Therapy
Repositório Institucional da USP (Biblioteca Digital da Produção Intelectual)
Universidade de São Paulo (USP)
instacron:USP
Repositório Institucional da USP (Biblioteca Digital da Produção Intelectual)
Universidade de São Paulo (USP)
instacron:USP
Chronic granulomatous disease (CGD) is an inherited primary immunodeficiency disorder characterised by recurrent and often life-threatening infections and hyperinflammation. It is caused by defects of the phagocytic NADPH oxidase, a multicomponent en
Autor:
Andrea Schejtman, Maren Weisser, David C. Thomas, Antonio Condino-Neto, Marta Zinicola, Giorgia Santilli, Adrian J. Thrasher, Walmir Cutrim Aragão Filho
Publikováno v:
Blucher Medical Proceedings.