Personalised Prophylaxis in a Child with Haemophilia A and Type 1 Diabetes

Autor: Maria Sol Cruz, Josefina Santillan, Julieta Lesser, Juan Pablo Ortiz, Laura Forzani

Publikováno v: Clinics and Practice, Vol 11, Iss 2, Pp 287-292 (2021)

Poor management of either type 1 diabetes or haemophilia A can lead to complications such as organ dysfunction and haemarthropathy. Here, we describe the case of an 8-year-old boy diagnosed with severe haemophilia A shortly after birth. At 2 years ol

Externí odkaz: https://doaj.org/article/ec145ccef183499e90bef05229a5f4af

Real-World Data on the Effectiveness and Safety of wilate for the Treatment of von Willebrand Disease

Autor: Sylvia Werner, Cesar Montaño Mejía, Hassan M. Yaish, George M. Rodgers, Kate Khair, Michelle Sholzberg, Jerome M. Teitel, Davide Matino, Zuzana Cermakova, Alpha Barrie, Mario von Depka Prondzinski, Maria Sol Cruz

Publikováno v: TH Open, Vol 05, Iss 03, Pp e264-e272 (2021)
TH Open: Companion Journal to Thrombosis and Haemostasis

Background The efficacy and safety of wilate (human von Willebrand factor/coagulation factor VIII) in patients with von Willebrand disease (VWD) has been demonstrated in clinical trials. Here, we present real-world data on the use of wilate for the r

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::016887afaa344c541c7fe8d7254aec51
https://doi.org/10.1055/s-0041-1730283

Using pharmacokinetics for tailoring prophylaxis in people with hemophilia switching between clotting factor products: A scoping review

Autor: Jacky K. Yu, Alfonso Iorio, Andrea N. Edginton, Sanjay Ahuja, Ma Teresa Álvarez Román, Ma E. Arrieta, Mikko Arola, Giovanni Barillari, Vinod Balasa, Mark Belletrutti, Ruben Berrueco Moreno, Philippe Beurrier, Cristoph Bidlingmaier, Victor Blanchette, Jan Blatny, Santiago Bonanad, Kelsey Brose, Deborah Brown, Paulette C. Byant, Mariana Canaro, Manuela Carvalho, Cristina Catarino, Meera Chitlur, Erin Cockrell, Pratima Chowdary, Marjon Cnossen, Peter Collins, Michial Coppens, Stacy Croteau, Dorina Cultrera, Raimundo de Cristofaro, Emmauelle de Raucourt, Dominique Desprez, Amy Dunn, Magda El‐Ekiabi, Barbara Faganel Kotnik, Kathleen Fischer, Brigit Frotscher, Susana Garbiero, Raquel Garrido Ruiz, Joan Gill, Carmen Gomez del Castillo, Saskia Gottstein, Giuseppe Lassandro, Paola Giordano, Daniel Hart, Inga Hegemann, Cedric Hermans, Baolai Hua, Nina Hwang, Shannon Jackson, Paula James, Olga Katsarou, Kaan Kavakli, Christine Kempton, Karim Kentouche, Osman Khan, Rainer Kobelt, Rebecca Kruse‐Jarres, Edward Laane, Eric Larson, Riitta Lassila, Adrienne Lee, Man‐Chiu Poon, Jennifer Lissick, Satu Langstrom, Johnny Mahlangu, Michael Makris, Emmanuela Marchesini, Jose Mateo, Pacual Marco Vera, Marta Martorell, Tadashi Matsushita, Simon McCrae, Eva Mignot‐Castellano, Caitlin Montcrieff, Philip Maes, Veerle Mondelars, Marlies Bekart, Elena Mora, Juan Cristóbal Morales, Guillaume Mourey, Marie Ann Bertrand, Mariasanta Napolitano, Sergio Siragusa, Claude Negrier, Daniela Neme, Ritta Niinimaki, Johannes Oldenburg, Thilo Albert, Deborah Ornstein, Margarete Ozelo, John Carl Panetta, Ellis J. Neufeld, Stephanie P'Ng, Kathelijne Peerlinck, Berardino Pollio, Claire Pouplard, Yves Gruel, Alessandra Prezotti, Vicky Price, Fitri Primacakti, Mathieu Puyade, Paolo Radossi, Leslie Raffini, Margaret Ragni, Savita Rangarajan, Mark T. Reding, Robin Reid, Jose Restrepo, Jose Ramirez, Michael Recht, Manuel Rodriguez Lopez, Arlette Ruiz‐Sàez, Mahasen Saleh, Amy Shapiro, Anjali Sharathkumar, Anna Selmeczi, Mindy Simpson, Tami Singleton, Maria Sol Cruz, Veronica Soto, MacGregor Steele, Werner Streif, Hao Wei Sun, Bruce Ritchie, Jing Sun, Xiaqin Feng, Takashi Suzuki, Asuza Nagao, Cliff Takemoto, Heather Tapp, Jerry Teitel, Alan Tinmouth, Courtney Thornburg, Alberto Tosseto, Oliver Turnstall, Catherine Vezina, Beth Warren, Allison Wheeler, Juan D. Wilches Gutierrez, John K.M. Wu, Tung Wynn, Renchi Yang, Guy Young, Ezio Zanon, Irena Zupan

Publikováno v: Research and practice in thrombosis and haemostasis, Vol. 3, no.3, p. 528-541 (2019)
Research and Practice in Thrombosis and Haemostasis
Research and Practice in Thrombosis and Haemostasis, Vol 3, Iss 3, Pp 528-541 (2019)

The objective of this scoping review is to summarize the current use of pharmacokinetics for tailoring prophylaxis in hemophilia patients switching between clotting factor products. Patients with hemophilia may require switching of clotting factor co

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8855ec59f7541838e90c9de25930d966
https://hdl.handle.net/2078.1/224098

Observational Study on Safety and Efficacy of Factor Replacement Therapy in the Management of Von Willebrand Disease Patients - Results from an Ongoing Study with a VWF/FVIII Concentrate

Autor: Sylvia Werner, Maria Sol Cruz, Kate Khair, Sigurd Knaub, Mario von Depka, Hassan M. Yaish, George M. Rodgers

Publikováno v: Blood. 128:4968-4968

Introduction and Objective Prospective surveillance studies are a useful tool to monitor drug safety and efficacy in the post-approval period and provide treaters and caregivers with real-life information about von Willebrand disease (VWD) treatment.

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_________::983766d083cd539a422f54e0c0d1e800
https://doi.org/10.1182/blood.v128.22.4968.4968