Zobrazeno 1 - 10
of 47
pro vyhledávání: '"Maria Rosa Lidonnici"'
Autor:
Maria Rosa Lidonnici, Ylenia Paleari, Francesca Tiboni, Giacomo Mandelli, Claudia Rossi, Michela Vezzoli, Annamaria Aprile, Carsten Werner Lederer, Alessandro Ambrosi, Franck Chanut, Francesca Sanvito, Andrea Calabria, Valentina Poletti, Fulvio Mavilio, Eugenio Montini, Luigi Naldini, Patrizia Cristofori, Giuliana Ferrari
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 11, Iss , Pp 9-28 (2018)
Gene therapy clinical trials require rigorous non-clinical studies in the most relevant models to assess the benefit-to-risk ratio. To support the clinical development of gene therapy for β-thalassemia, we performed in vitro and in vivo studies for
Externí odkaz:
https://doaj.org/article/fa7c8bf590fd4385824802dbcaeebd2f
Autor:
Antonella Nai, Maria Rosa Lidonnici, Giorgia Federico, Mariateresa Pettinato, Violante Olivari, Federica Carrillo, Simonetta Geninatti Crich, Giuliana Ferrari, Clara Camaschella, Laura Silvestri, Francesca Carlomagno
Publikováno v:
Haematologica, Vol 106, Iss 3 (2020)
The Nuclear Receptor Coactivator 4 (NCOA4) promotes ferritin degradation and Ncoa4-ko mice in C57BL/6 background show microcytosis and mild anemia, aggravated by iron deficiency. To understand tissue specific contribution of NCOA4-mediated ferritinop
Externí odkaz:
https://doaj.org/article/b4271343b7a34463b76c59669b198260
Autor:
Erika Zonari, Giacomo Desantis, Carolina Petrillo, Francesco E. Boccalatte, Maria Rosa Lidonnici, Anna Kajaste-Rudnitski, Alessandro Aiuti, Giuliana Ferrari, Luigi Naldini, Bernhard Gentner
Publikováno v:
Stem Cell Reports, Vol 8, Iss 4, Pp 977-990 (2017)
Summary: Ex vivo gene therapy based on CD34+ hematopoietic stem cells (HSCs) has shown promising results in clinical trials, but genetic engineering to high levels and in large scale remains challenging. We devised a sorting strategy that captures mo
Externí odkaz:
https://doaj.org/article/c4223e2bc0bd429f94300fc4ee6e9977
Autor:
Irene Artuso, Mariateresa Pettinato, Antonella Nai, Alessia Pagani, Ugo Sardo, Benjamin Billoré, Maria Rosa Lidonnici, Cavan Bennett, Giacomo Mandelli, Sant-Rayn Pasricha, Giuliana Ferrari, Clara Camaschella, Léon Kautz, Laura Silvestri
Publikováno v:
Haematologica, Vol 104, Iss 3 (2019)
Externí odkaz:
https://doaj.org/article/7006108ef81a474cb5c49c5a3f4bf1b2
Autor:
Maria Rosa Lidonnici, Annamaria Aprile, Marta Claudia Frittoli, Giacomo Mandelli, Ylenia Paleari, Antonello Spinelli, Bernhard Gentner, Matilde Zambelli, Cristina Parisi, Laura Bellio, Elena Cassinerio, Laura Zanaboni, Maria Domenica Cappellini, Fabio Ciceri, Sarah Marktel, Giuliana Ferrari
Publikováno v:
Haematologica, Vol 102, Iss 4 (2017)
Externí odkaz:
https://doaj.org/article/1cbe996887dd4a61a85712cff198362b
Supplementary Figure Legends from The Dispersal of Replication Proteins after Etoposide Treatment Requires the Cooperation of Nbs1 with the Ataxia Telangiectasia Rad3-Related/Chk1 Pathway
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1a117d2507c4a82c34631d1e8c6f84c3
https://doi.org/10.1158/0008-5472.22367063
https://doi.org/10.1158/0008-5472.22367063
In mammalian cells, DNA replication takes place in functional subnuclear compartments, called replication factories, where replicative factors accumulate. The distribution pattern of replication factories is diagnostic of the different moments (early
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1ed18d1317ac90e96f0cadea85e61069
https://doi.org/10.1158/0008-5472.c.6495407.v1
https://doi.org/10.1158/0008-5472.c.6495407.v1
Supplementary Figure 2 from The Dispersal of Replication Proteins after Etoposide Treatment Requires the Cooperation of Nbs1 with the Ataxia Telangiectasia Rad3-Related/Chk1 Pathway
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::062058699dd6c30a17042ea200b1209e
https://doi.org/10.1158/0008-5472.22367066
https://doi.org/10.1158/0008-5472.22367066
Autor:
Bruno Calabretta, Tessa L. Holyoake, Robert V. Martinez, Ying Zhang, Nick Donato, Todd Waldron, Giovanna Ferrari-Amorotti, Marco Prisco, Angela Rachele Soliera, Alessandra Audia, Maria Rosa Lidonnici
Ectopic expression of CAAT/enhancer binding protein α (C/EBPα) in p210BCR/ABL-expressing cells induces granulocytic differentiation, inhibits proliferation, and suppresses leukemogenesis. To dissect the molecular mechanisms underlying these biologi
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::49ef21abb2bd490ab81728ff36581129
https://doi.org/10.1158/0008-5472.c.6500832
https://doi.org/10.1158/0008-5472.c.6500832
Supplementary Figure 1 from The Dispersal of Replication Proteins after Etoposide Treatment Requires the Cooperation of Nbs1 with the Ataxia Telangiectasia Rad3-Related/Chk1 Pathway
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::101e9500e08de43b90ed2daf3f603164
https://doi.org/10.1158/0008-5472.22367069.v1
https://doi.org/10.1158/0008-5472.22367069.v1