Lived experiences of patients with distal renal tubular acidosis treated with ADV7103 and of their caregivers: a qualitative study

Autor: Michaël Acquadro, Alexia Marrel, Maria A. Manso-Silván, Catherine Guittet, Sophie Joukoff, Aurélia Bertholet-Thomas

Publikováno v: Orphanet Journal of Rare Diseases, Vol 17, Iss 1, Pp 1-8 (2022)

Abstract Background Consequences of distal renal tubular acidosis (dRTA) on growth, bone and kidney, sometimes associated with hearing loss, may significantly affect quality of life (QoL). This descriptive qualitative study explores QoL linked to dRT

Externí odkaz: https://doaj.org/article/414cef9ae7f847e5ab5de297029975e9

Bone mineral density and growth changes in patients with distal renal tubular acidosis after two-years treatment with a new alkalizing drug (ADV7103)

Autor: Aurélia Bertholet-Thomas, Maria A. Manso-Silván, Victor Navas-Serrano, Catherine Guittet, Sophie Joukoff, Justine Bacchetta, Olivia Boyer, Mariano Rodriguez Portillo, Luc-André Granier

Publikováno v: Nefrologia.

ADV7103 is a new prolonged-release treatment for distal renal tubular acidosis (dRTA), containing potassium citrate and potassium bicarbonate. Since acidosis may affect bone mineral contents, the effects of ADV7103 on bone mineral density (BMD) and g

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::629cd3c0be8b5a301326ae821a682788
https://pubmed.ncbi.nlm.nih.gov/36529656

Efficacy and safety of an innovative prolonged-release combination drug in patients with distal renal tubular acidosis: an open-label comparative trial versus standard of care treatments

Autor: Aurélia Bertholet-Thomas, Catherine Guittet, Maria A. Manso-Silván, Arnaud Castang, Véronique Baudouin, Mathilde Cailliez, Massimo Di Maio, Olivia Gillion-Boyer, Emilija Golubovic, Jérôme Harambat, Alexandre Klein, Bertrand Knebelmann, François Nobili, Robert Novo, Ludmila Podracka, Gwenaëlle Roussey-Kesler, Christos Stylianou, Luc-André Granier

Publikováno v: Pediatric Nephrology
Pediatric Nephrology, Springer Verlag, 2021, 36 (1), pp.83-91. ⟨10.1007/s00467-020-04693-2⟩
Pediatr Nephrol
Pediatric Nephrology (Berlin, Germany)

Background Distal renal tubular acidosis (dRTA), due to impaired acid secretion in the urine, can lead to severe long-term consequences. Standard of care (SoC) oral alkalizers, requiring several daily intakes, are currently used to restore normal pla

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a9b13607d53a3dbd1d8d6afbe0cb4bc1
https://hal.archives-ouvertes.fr/hal-03154797

Correction to: Efficacy and safety of an innovative prolonged-release combination drug in patients with distal renal tubular acidosis: an open-label comparative trial versus standard of care treatments

Autor: Massimo Di Maio, Véronique Baudouin, Alexandre Klein, Robert Novo, Aurélia Bertholet-Thomas, Emilija Golubovic, Jérôme Harambat, François Nobili, Ludmila Podracka, Bertrand Knebelmann, Maria A. Manso-Silván, Luc-André Granier, Olivia Gillion-Boyer, Gwenaëlle Roussey-Kesler, Catherine Guittet, Arnaud Castang, Christos Stylianou, Mathilde Cailliez

Publikováno v: Pediatric Nephrology. 36:215-215

Distal renal tubular acidosis (dRTA), due to impaired acid secretion in the urine, can lead to severe long-term consequences. Standard of care (SoC) oral alkalizers, requiring several daily intakes, are currently used to restore normal plasma bicarbo

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3a8f312bff4c55883da47c08d005d2b7
https://doi.org/10.1007/s00467-020-04776-0