Zobrazeno 1 - 10
of 30
pro vyhledávání: '"Marcella, Facchini"'
Autor:
Francesca Fumagalli, Valeria Calbi, Fabiola De Mattia, Alberto Zambon, Vera Gallo, Salvatore Recupero, Elena Sophia Fratini, Alessia Ippolito, Francesca Ciotti, Maddalena Fraschini, Marina Sarzana, Stefano Scarparo, Eugenio Montini, Sara Locatelli, Marcella Facchini, Alessandra Clerici, Francesco Morena, Sabata Martino, Muska Yarzi, Sean Moro, Andrew Shenker, Jean Brooks, Alan Richardson, Leslie Meltzer, Laura Campbell, Alessandro Aiuti
Publikováno v:
Genetics in Medicine Open, Vol 2, Iss , Pp 100882- (2024)
Externí odkaz:
https://doaj.org/article/754fbeb348e443f3bc199e31def8215a
Autor:
Bernhard, Gentner, Francesca, Tucci, Stefania, Galimberti, Francesca, Fumagalli, Maurizio, De Pellegrin, Paolo, Silvani, Chiara, Camesasca, Silvia, Pontesilli, Silvia, Darin, Francesca, Ciotti, Marina, Sarzana, Giulia, Consiglieri, Chiara, Filisetti, Giulia, Forni, Laura, Passerini, Daniela, Tomasoni, Daniela, Cesana, Andrea, Calabria, Giulio, Spinozzi, Maria-Pia, Cicalese, Valeria, Calbi, Maddalena, Migliavacca, Federica, Barzaghi, Francesca, Ferrua, Vera, Gallo, Simona, Miglietta, Erika, Zonari, Patali S, Cheruku, Claudia, Forni, Marcella, Facchini, Ambra, Corti, Michela, Gabaldo, Stefano, Zancan, Serena, Gasperini, Attilio, Rovelli, Jaap-Jan, Boelens, Simon A, Jones, Robert, Wynn, Cristina, Baldoli, Eugenio, Montini, Silvia, Gregori, Fabio, Ciceri, Maria G, Valsecchi, Giancarlo, la Marca, Rossella, Parini, Luigi, Naldini, Alessandro, Aiuti, Maria-Ester, Bernardo, Ilaria, Visagalli
Publikováno v:
New England Journal of Medicine. 385:1929-1940
Background Allogeneic hematopoietic stem-cell transplantation is the standard of care for Hurler syndrome (mucopolysaccharidosis type I, Hurler variant [MPSIH]). However, this treatment is only partially curative and is associated with complications.
Autor:
Francesca Fumagalli, Valeria Calbi, Fabiola De Mattia, Alberto A. Zambon, Vera Gallo, Salvatore Recupero, Cristina Baldoli, Elena Sophia Fratini, Francesca Ciotti, Maddalena Fraschini, Marina Sarzana, Stefano Scarparo, Andrea Calabria, Eugenio Montini, Sara Locatelli, Marcella Facchini, Alessandra Clerici, Francesco Morena, Sabata Martino, Angelica Claros, Arpeat Kaviya, Sean Moro, Jean Brooks, Alan Richardson, Alessandro Aiuti
Publikováno v:
Molecular Genetics and Metabolism. 138:107108
Autor:
Sonya C. Carnell, John D. Perry, Lee Borthwick, Daniela Vollmer, Jacob Biboy, Marcella Facchini, Alessandra Bragonzi, Alba Silipo, Annette C. Vergunst, Waldemar Vollmer, Anjam C. M. Khan, Anthony De Soyza
Publikováno v:
International Journal of Molecular Sciences, Vol 19, Iss 6, p 1604 (2018)
Burkholderia cepacia complex (BCC) bacteria are a group of opportunistic pathogens that cause severe lung infections in cystic fibrosis (CF). Treatment of BCC infections is difficult, due to the inherent and acquired multidrug resistance of BCC. Ther
Externí odkaz:
https://doaj.org/article/7a500e3c60b14462b14aaec24a757257
Autor:
Maddalena Migliavacca, Paola Massariello, Roberto Miniero, Laura Lorioli, Laura Castagnaro, Francesca Tucci, Francesca Fumagalli, Francesco Calzatini, Miriam Casiraghi, Luca Santoleri, Claudia Fossati, Daniele Canarutto, Marcella Facchini, Maria Pia Cicalese, Fabio Ciceri, Alessandra Biffi, Matilde Zambelli, Sarah Marktel, Valeria Calbi, Stefano Zancan, Marta Claudia Frittoli, Paolo Silvani, Gigliola Antonioli, Giulia Consiglieri, Raffaella Milani, Silvia Darin, Francesca Ferrua, Salvatore Recupero, Maria Ester Bernardo, Salvatore Gattillo, Rossana Fiori, Alessandro Aiuti, Federica Barzaghi, Michele Manfredini
Publikováno v:
Bone marrow transplantation
Collection of an adequate amount of autologous haematopoietic stem progenitor cells (HSPC) is required for ex vivo manipulation and successful engraftment for certain inherited disorders. Fifty-seven paediatric patients (age 0.5–11.4 years) underwe
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::64af600a2b198d4c7df83ce154616c32
http://www.nature.com/bmt/index.html
http://www.nature.com/bmt/index.html
Autor:
Marina Sarzana, Massimo Filippi, Valeria Calbi, Vera Gallo, Francesca Fumagalli, Stefano Zancan, Jesus Segovia, Elena Fratini, Gigliola Antonioli, Maria Sessa, Sara Locatelli, Maria Grazia Natali Sora, Fabio Ciceri, Alessandro Aiuti, Alessandra Biffi, Maria Pia Cicalese, Marcella Facchini, Luigi Naldini, Alberto A. Zambon, Gerald Downey, Maria Ester Bernardo, Laetitia C. Schwab, Francesca Ciotti
Publikováno v:
Molecular Genetics and Metabolism. 132:S40
Akademický článek
Tento výsledek nelze pro nepřihlášené uživatele zobrazit.
K zobrazení výsledku je třeba se přihlásit.
K zobrazení výsledku je třeba se přihlásit.
Repurposing the antimycotic drug flucytosine for suppression of Pseudomonas aeruginosa pathogenicity
Autor:
Livia Leoni, Paolo Visca, Francesco Imperi, Marcella Facchini, Alessandra Bragonzi, Emanuela Frangipani, Daniela Visaggio, Francesco Massai
Publikováno v:
Proceedings of the National Academy of Sciences. 110:7458-7463
Although antibiotic resistance represents a public health emergency, the pipeline of new antibiotics is running dry. Repurposing of old drugs for new clinical applications is an attractive strategy for drug development. We used the bacterial pathogen
Autor:
Pauline E. Misson, Alice Rossi, Serena Ranucci, Alessandra Bragonzi, Beatriz Alcalá-Franco, Eric Chevalier, Francesca Bernardini, Cristina Cigana, Daniel Obrecht, Marcella Facchini, Camilla Riva, Michel Schmitt, Glenn E. Dale, Ida De Fino, Maj Brodmann, Achim Wach
The clinical development of antibiotics with a new mode of action combined with efficient pulmonary drug delivery is a priority against untreatable Pseudomonas aeruginosa lung infections. POL7001 is a macrocycle antibiotic belonging to the novel clas
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ae9e70f16832a8a9115aaaadbaf2183f
https://europepmc.org/articles/PMC4958219/
https://europepmc.org/articles/PMC4958219/
Autor:
Marcella Facchini, Fabrizia Minandri, Paolo Pasquali, Alessandra Bragonzi, Francesco Imperi, Emanuela Frangipani, Carlo Bonchi, Paolo Visca, Daniela Visaggio
Pseudomonas aeruginosa is a leading cause of hospital-acquired pneumonia and chronic lung infections in cystic fibrosis patients. Iron is essential for bacterial growth, and P. aeruginosa expresses multiple iron uptake systems, whose role in lung inf
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f0c6a18e26bb4d5a0311768766dcf1cd
http://hdl.handle.net/11573/928791
http://hdl.handle.net/11573/928791