Adapting traditional content validation methods to fit purpose : an example with a novel video assessment and training materials in Duchenne muscular dystrophy (DMD)

Autor: White, Michelle K., Leffler, Mindy, Rychlec, Kaitlin, Jones, Chris, McSherry, Christine, Walker, Linsey, Kosinski, Mark

Publikováno v: Quality of Life Research, 2019 Nov 01. 28(11), 2979-2988.

Externí odkaz: https://www.jstor.org/stable/48705225

Implications of Pediatric Initiatives on CNS Drug Development for All Ages—2020 and Beyond: Second of Three Sets of Expanded Proceedings from the 2020 ISCTM Autumn Conference on Pediatric Drug Development

Autor: Pandina, Gahan, Busner, Joan, Horrigan, Joseph P., McSherry, Christine, Bateman-House, Alison, Pani, Luca, Kando, Judith

Publikováno v: Innov Clin Neurosci

This article expands upon a session, titled “Implications of Pediatric Initiatives on CNS Drug Development for All Ages—2020 and Beyond,” that was presented as part of a two-day meeting on pediatric drug development at the International Society

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=pmid________::8106e887b86c1bc418993b9e96116b9b
https://europepmc.org/articles/PMC10132276/

Implications of Pediatric Initiatives on CNS Drug Development for All Ages-2020 and Beyond: Second of Three Sets of Expanded Proceedings from the 2020 ISCTM Autumn Conference on Pediatric Drug Development.

Autor: Pandina G; Dr. Pandina is with Janssen Pharmaceuticals in Titusville, New Jersey., Busner J; Dr. Busner is with Signant Health in Blue Bell, Pennsylvania and Department of Psychiatry, Virginia Commonwealth University School of Medicine in Richmond, Virginia., Horrigan JP; Dr. Horrigan is Chief Medical Officer, AMO Pharma, Ltd. in Wonersh, United Kingdom and Consulting Associate Professor, Duke University in Durham, North Carolina., McSherry C; Ms. McSherry is Founder, Jett Foundation, and Co-founder and Chief Executive Officer, Casimir, LLC in Plymouth, Massachusetts., Bateman-House A; Dr. Bateman-House is with New York University Grossman School of Medicine in New York City, New York., Pani L; Dr. Pani is former Director General, Italian Medicines Agency (AIFA), former Committee for Medicinal Products for Human Use (CHMP) member, and former Scientific Advice Working Party (SAWP) member, European Medicines Agency (EMA); he is with the University of Miami in Miami, Florida, and VeraSci in Durham, North Carolina., Kando J; Dr. Kando is with Tris Pharmaceuticals in Monmouth Junction, New Jersey.

Publikováno v: Innovations in clinical neuroscience [Innov Clin Neurosci] 2023 Jan-Mar; Vol. 20 (1-3), pp. 18-24.