Zobrazeno 1 - 10
of 196
pro vyhledávání: '"Leonard A Valentino"'
Patient-centered pharmacovigilance: priority actions from the inherited bleeding disorders community
Autor:
Fiona Robinson, Sonji Wilkes, Nathan Schaefer, Miriam Goldstein, Michelle Rice, Johanna Gray, Sharon Meyers, Leonard A. Valentino
Publikováno v:
Therapeutic Advances in Drug Safety, Vol 14 (2023)
Pharmacovigilance, the science and practice of monitoring the effects of medicinals and their safety, is the responsibility of all stakeholders involved in the development, manufacture, regulation, distribution, prescription, and use of drugs and dev
Externí odkaz:
https://doaj.org/article/76da07539fdf4f8dafcd2a2105cf4f5f
Publikováno v:
Research and Practice in Thrombosis and Haemostasis, Vol 5, Iss 6, Pp n/a-n/a (2021)
Abstract Gene therapy is at the forefront of the drive to bring the potential of cure to patients with genetic diseases. Multiple mechanisms of effective and efficient gene therapy delivery (eg, lentiviral, adeno‐associated) for transgene expressio
Externí odkaz:
https://doaj.org/article/1678b4b4d87d4bcba6864f03265dfccd
Publikováno v:
Expert Review of Hematology. 16:1-5
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::321c6becf405db166bed802ded36b8ca
https://doi.org/10.1080/17474086.2023.2178412
https://doi.org/10.1080/17474086.2023.2178412
Publikováno v:
Expert Review of Hematology. 16:129-134
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::5f75ef55872e30f27d7cb2c1fd02dee8
https://doi.org/10.1080/17474086.2023.2181782
https://doi.org/10.1080/17474086.2023.2181782
Autor:
Jill M. Johnsen, Shelley N. Fletcher, Angela Dove, Haley McCracken, Beth K. Martin, Martin Kircher, Neil C. Josephson, Jay Shendure, Sarah E. Ruuska, Leonard A. Valentino, Glenn F. Pierce, Crystal Watson, Dunlei Cheng, Michael Recht, Barbara A. Konkle
Publikováno v:
Journal of Thrombosis and Haemostasis. 20:2022-2034
Hemophilia A (HA) and hemophilia B (HB) are rare inherited bleeding disorders. Although causative genetic variants are clinically relevant, in 2012 only 20% of US patients had been genotyped.My Life, Our Future (MLOF) was a multisector cross-sectiona
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bd83930bf42172f5f590a617c4039729
https://doi.org/10.1111/jth.15805
https://doi.org/10.1111/jth.15805
Autor:
Mark T. Reding, Judith Baker, Michael Recht, Miguel A. Escobar, Leonard A. Valentino, Joseph N Pugliese, Constance B Thibodeaux, Mark W. Skinner, Diane J. Nugent, Susan Karp, Michelle Rice, Regina Butler, Neil Frick, Kollet Koulianos, Susan Lattimore
Publikováno v:
Journal of Blood Medicine
Rare, chronic diseases such as hemophilia and other congenital coagulation disorders require coordinated delivery of services for optimal outcomes. Hemophilia Treatment Centers (HTCs) are specialized, multidisciplinary health-care centers providing t
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e773707621f0189473d59b8b1becb5a1
http://europepmc.org/articles/PMC8544265
http://europepmc.org/articles/PMC8544265
Publikováno v:
Arch Bone Jt Surg
This article examines the elements that affect the return to sport (RTS) and the risk and percentages of reinjury following a prior primary anterior cruciate ligament reconstruction (ACLR). The prevalence of RTS following ACLR ranges from 71% to 83%.
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=pmid________::f5f724bbd4e6db15ee0b3931ce551682
https://pubmed.ncbi.nlm.nih.gov/36258743
https://pubmed.ncbi.nlm.nih.gov/36258743
Publikováno v:
Biologics : Targets & Therapy
Progress in hemophilia therapy has been remarkable in the first 20 years of the third millennium, but the innovation began with the description the fractionation of plasma in 1946. The first concentrates followed the discovery of FVIII in the cryopre
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::eb174d070a4b1b2907c531aadebf9ca3
http://europepmc.org/articles/PMC8214539
http://europepmc.org/articles/PMC8214539
Autor:
Leonard A. Valentino
Publikováno v:
Expert Review of Hematology. :1-1
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::df3a87e32cc1d0edcadcd94415895588
https://doi.org/10.1080/17474086.2023.2218612
https://doi.org/10.1080/17474086.2023.2218612
Autor:
Victor S. Blanchette, Brian O'Mahony, Mark W. Skinner, Thomas Sannié, Claude Negrier, Val Bias, Leonard A. Valentino
Publikováno v:
The Journal of Haemophilia Practice. 8:69-79
The current standard of care for treating people with haemophilia (PWH) in the developed world is prophylaxis with regular infusions of clotting factor concentrates. Gene therapy is being investigated as a new treatment paradigm for haemophilia and i
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::89a0a23a6536594cad17564ddefe6e6e
https://doi.org/10.17225/jhp00178
https://doi.org/10.17225/jhp00178