Psychometric evaluation of the PROMIS parent proxy mobility item bank for use in Duchenne muscular dystrophy.

Autor: Lowes LP; Center for Gene Therapy, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, USA., Le Reun CM; Biostatistics, Sainte-Anne, Guadeloupe, France., Alfano LN; Center for Gene Therapy, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, USA., Reash NF; Center for Gene Therapy, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, USA., Iammarino MA; Center for Gene Therapy, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, USA., Patel S; Patient-Centered Outcomes, Sarepta Therapeutics, Inc., Cambridge, MA, USA., Audhya IF; Patient-Centered Outcomes, Sarepta Therapeutics, Inc., Cambridge, MA, USA.

Publikováno v: Developmental medicine and child neurology [Dev Med Child Neurol] 2024 Dec 19. Date of Electronic Publication: 2024 Dec 19.