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pro vyhledávání: '"LaRusso LB"'
Autor:
Graham RJ; Department of Anesthesiology, Critical Care and Pain Medicine, Division of Critical Care Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA beggs@enders.tch.harvard.edu robert.graham@childrens.harvard.edu., Muntoni F; The Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health and NIHR Great Ormond Street Hospital Biomedical Research Centre, London, UK., Hughes I; Royal Manchester Children's Hospital, Manchester, UK., Yum SW; Children's Hospital of Philadelphia, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania, USA., Kuntz NL; Ann and Robert H Lurie Children's Hospital of Chicago, Chicago, Illinois, USA., Yang ML; Children's Hospital Colorado, Aurora, Colorado, USA., Byrne BJ; Children's Research Institute, University of Florida, Gainesville, Florida, USA., Prasad S; Audentes Therapeutics, San Francisco, California, USA., Alvarez R; Cure CMD, Torrance, California, USA., Genetti CA; Division of Genetics and Genomics, The Manton Center for Orphan Disease Research, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA., Haselkorn T; EpiMetrix, Los Altos, California, USA., James ES; Audentes Therapeutics, San Francisco, California, USA., LaRusso LB; Chestnut Medical Communications, Walpole, Massachusetts, USA., Noursalehi M; Audentes Therapeutics, San Francisco, California, USA., Rico S; Audentes Therapeutics, San Francisco, California, USA., Beggs AH; Division of Genetics and Genomics, The Manton Center for Orphan Disease Research, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA beggs@enders.tch.harvard.edu robert.graham@childrens.harvard.edu.
Publikováno v:
Archives of disease in childhood [Arch Dis Child] 2020 Apr; Vol. 105 (4), pp. 332-338. Date of Electronic Publication: 2019 Sep 04.