Zobrazeno 1 - 4
of 4
pro vyhledávání: '"Kristen N. Vondrak"'
Autor:
Steven Q. Le, Shih-hsin Kan, Don Clarke, Valentina Sanghez, Martin Egeland, Kristen N. Vondrak, Terence M. Doherty, Moin U. Vera, Michelina Iacovino, Jonathan D. Cooper, Mark S. Sands, Patricia I. Dickson
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 8, Iss C, Pp 42-51 (2018)
Antibodies against recombinant proteins can significantly reduce their effectiveness in unanticipated ways. We evaluated the humoral response of mice with the lysosomal storage disease mucopolysaccharidosis type I treated with weekly intravenous reco
Externí odkaz:
https://doaj.org/article/458c35de4ec1464eb7de993788d68d45
Autor:
Moin Vera, Terence M. Doherty, Shih hsin Kan, Kristen N. Vondrak, Michelina Iacovino, Martin T. Egeland, Steven Q. Le, Patricia I. Dickson, Jonathan D. Cooper, Mark S. Sands, Valentina Sanghez, Don Clarke
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 8, Iss C, Pp 42-51 (2018)
Molecular Therapy. Methods & Clinical Development
Molecular Therapy. Methods & Clinical Development
Antibodies against recombinant proteins can significantly reduce their effectiveness in unanticipated ways. We evaluated the humoral response of mice with the lysosomal storage disease mucopolysaccharidosis type I treated with weekly intravenous reco
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::03b3e4be0fe91d6ae9802b52e6703012
http://www.sciencedirect.com/science/article/pii/S2329050117301079
http://www.sciencedirect.com/science/article/pii/S2329050117301079
Autor:
Patti Dickson, Michelina Iacovino, Don Clarke, Kristen N. Vondrak, Shih-hsin Kan, Steven Q. Le, Mark S. Sands, Valentina Sanghez, Moin Vera
Publikováno v:
Molecular Genetics and Metabolism. 120:S118
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::b048f3c72ad68aa0ef23d06858ec115d
https://doi.org/10.1016/j.ymgme.2016.11.305
https://doi.org/10.1016/j.ymgme.2016.11.305
Autor:
Shih-hsin Kan, Zhi Chen, Stuart Bunting, Brett E. Crawford, Wesley Wong, Anil Bagri, Evan G. Adintori, John Holtzinger, Melanie J. Lo, Elizabeth F. Neufeld, Danielle Crippen-Harmon, Paul A. Fitzpatrick, Jillian R. Brown, Josh C. Woloszynek, Pascale M.N. Tiger, Kristen N. Vondrak, Diana S. Cheung, Kazuhiro Ohmi, Jon Vincelette, Sherry Bullens, Jonathan H. LeBowitz, Chuck Hague, Steven Q. Le, Roger Lawrence, Terri Christianson, Bryan K. Yip, Daniel J. Wendt, Katherine A. Webster, Mika Aoyagi-Scharber, Patricia I. Dickson
Publikováno v:
Proceedings of the National Academy of Sciences of the United States of America, vol 111, iss 41
Mucopolysaccharidosis type IIIB (MPS IIIB, Sanfilippo syndrome type B) is a lysosomal storage disease characterized by profound intellectual disability, dementia, and a lifespan of about two decades. The cause is mutation in the gene encoding α–N-
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f6e9cef317d3d7e5f182f493e8a4dd4c
https://europepmc.org/articles/PMC4205671/
https://europepmc.org/articles/PMC4205671/
