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pro vyhledávání: '"Kim Zaraspe"'
Autor:
Haiyan Fu, Kim Zaraspe, Naoko Murakami, Aaron S. Meadows, Ricardo J. Pineda, Douglas M. McCarty, Joseph Muenzer
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 10, Iss , Pp 327-340 (2018)
No treatment is available to address the neurological need and reversibility of MPS II. We developed a scAAV9-hIDS vector to deliver the human iduronate-2-sulfatase gene and test it in mouse model. We treated MPS II mice at different disease stages w
Externí odkaz:
https://doaj.org/article/b6032df5c230489cb9ac22b8477098f0
Autor:
Ricardo J. Pineda, Kim Zaraspe, Naoko Murakami, Aaron S. Meadows, Joseph Muenzer, Haiyan Fu, Douglas M. McCarty
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 10, Iss, Pp 327-340 (2018)
No treatment is available to address the neurological need and reversibility of MPS II. We developed a scAAV9-hIDS vector to deliver the human iduronate-2-sulfatase gene and test it in mouse model. We treated MPS II mice at different disease stages w
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9e6dbc0bd08344be9618482d88e5dcbc
http://www.sciencedirect.com/science/article/pii/S2329050118300688
http://www.sciencedirect.com/science/article/pii/S2329050118300688