Zobrazeno 1 - 7
of 7
pro vyhledávání: '"Karen Pinachyan"'
Autor:
Björn Vandewalle, Giancarlo Castaman, Maria Teresa Álvarez-Román, Carmen Escuriola Ettingshausen, László Nemes, Radovan Tomic, Paulo Martins, Joana F. Rodrigues, Karen Pinachyan
Publikováno v:
Scientific Reports, Vol 14, Iss 1, Pp 1-10 (2024)
Abstract An important aspect of improving care for people with hemophilia B (HB) is developing optimal treatment strategies. Here we aimed to provide in-silico evidence, comparing the estimated optimal posology of factor IX (FIX) products to support
Externí odkaz:
https://doaj.org/article/39c2268e6eaf4d91b011e4c904c5deca
Autor:
Wolfgang Miesbach, Greta Mulders, Daan Breederveld, Karen Pinachyan, Sandra Le Quellec, Ingrid Pabinger
Publikováno v:
Orphanet Journal of Rare Diseases, Vol 19, Iss 1, Pp 1-10 (2024)
Abstract Background Adeno-associated virus (AAV)-based gene therapy for haemophilia has advanced substantially in the last 13 years; recently, three products have received approvals from regulatory authorities. Although the impact on quality of life
Externí odkaz:
https://doaj.org/article/8ffb5b42aa32428096d4d247c35af0e4
Autor:
Martin Olivieri, Mindy Simpson, Songkai Yan, Johanna Fedorovsky, Xiang Zhang, Radovan Tomic, Karen Pinachyan, Maria Elisa Mancuso
To evaluate real-world annualized bleeding rates (ABRs), dosing frequency, and factor consumption of four recombinant FVIII (rFVIII) products using pooled data from centers in the US, Germany, and Italy. De-identified patient medical chart data were
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::887b163b41c12dcbbfe662e489147475
Autor:
Rima de Sahb-Berkovitch, Marie-Christine Woronoff-Lemsi, Mathieu Molimard, Jean-Pierre Armand, Marc Bardou, Loïc Bergougnoux, Christine Bouchet, Dominic Cellier, Bachir Dahmani, Bertrand Diquet, Thierry Lecomte, Nathalie Hoog Labouret, Claire Labreveux, François Meyer, Gilles Paintaud, Pascal Piedbois, Martine Pigeon, Olivier Amédée Manesme, Rémy Defrance, Dominique Tonelli, Karen Pinachyan, Sophie Tardieu
Publikováno v:
Therapies. 65:367-372
Resume L’evaluation pour l’admission au remboursement faite par la Commission de la Transparence de la Haute Autorite de Sante (HAS) comporte une cotation du Service Medical Rendu (SMR) qui donne l’acces au remboursement, de l’Amelioration du
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::58e38b851e65646ab4065e14c8123256
https://doi.org/10.2515/therapie/20010041
https://doi.org/10.2515/therapie/20010041
Autor:
Dominique Deplanque, Guillaume Birraux, Pierre-Henri Bertoye, Éric Postaire, Béatrice Barraud, Joëlle Benessiano, Ingrid Callies, Henri Caplain, Bruno Clément, Georges Dagher, Lauren Demerville, Anne-Marie Duguet, Catherine Durette, Dominique Figarella-Branger, Laurence Fluckiger, Elisabeth Frija-Orvoen, Coraline Gadras, Patrick Gelé, Jean-Marc Laurent-Vo, François Lemaire, Christian Libersa, Marie-Élise Llau, Olivier Louvet, Jean-Philippe Merlio, Armelle Mijonnet, Jean Petitpré, Alain Pierré, Karen Pinachyan, Jean-Charles Reynier, Anabelle Sailly, Pierre Schiavi, Tabassome Simon, Anne Vidal
Publikováno v:
Therapies. 64:259-267
The collection of human biological samples is of major importance for future research in France and Europe. In recent years, new regulatory procedures have been designed to monitor these activities; but they are somewhat complex and some clarificatio
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f264d42857b5f49f6e373cfc39f14b63
https://doi.org/10.2515/therapie/2009046
https://doi.org/10.2515/therapie/2009046
Autor:
Dominique Deplanque, Guillaume Birraux, Pierre-Henri Bertoye, Éric Postaire, Béatrice Barraud, Joëlle Benessiano, Ingrid Callies, Henri Caplain, Bruno Clément, Georges Dagher, Lauren Demerville, Anne Marie Duguet, Catherine Durette, Dominique Figarella-Branger, Laurence Fluckiger, Élisabeth Frija-Orvoen, Coraline Gadras, Patrick Gelé, Jean-Marc Laurent-Vo, François Lemaire, Christian Libersa, Marie-Élise Llau, Olivier Louvet, Jean-Philippe Merlio, Armelle Mijonnet, Jean Petitpré, Alain Pierré, Karen Pinachyan, Jean-Charles Reynier, Anabelle Sailly, Pierre Schiavi, Tabassome Simon, Anne Vidal
Publikováno v:
Therapies. 64:215-224
La constitution de collections d'echantillons biologiques humains a des fins scientifiques constitue un enjeu majeur en France et en Europe. Dans ce contexte, ces dernieres annees ont ete marquees par la volonte de mettre en place un meilleur encadre
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::10d55bea49217f1848f93d0ba61b3970
https://doi.org/10.2515/therapie/2009039
https://doi.org/10.2515/therapie/2009039
Autor:
Rima de Sahb-Berkovitch, Marie-Christine Woronoff-Lemsi, Mathieu Molimard, Jean-Pierre Armand, Marc Bardou, Loïc Bergougnoux, Christine Bouchet, Dominic Cellier, Bachir Dahmani, Bertrand Diquet, Thierry Lecomte, Nathalie Hoog Labouret, Claire Labreveux, François Meyer, Gilles Paintaud, Pascal Piedbois, Martine Pigeon, Olivier Amédée Manesme, Rémy Defrance, Dominique Tonelli, Karen Pinachyan, Sophie Tardieu
Publikováno v:
Therapie. 65(4)
Reimbursement is assessed by the Transparency Commission from the Health Authority (HAS) using a medical benefit (SMR) score that gives access to reimbursement, an "improvement of medical service rendered" (ASMR) that determines the added therapeutic
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b2d09138534c457d7bd70846f10d1f4c
https://pubmed.ncbi.nlm.nih.gov/20854761
https://pubmed.ncbi.nlm.nih.gov/20854761