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pro vyhledávání: '"John E Rasko"'
Autor:
Alexis A. Thompson, John E Rasko, Suradej Hongeng, Janet L. Kwiatkowski, Gary Schiller, Christof von Kalle, Marina Cavazzana, Philippe Leboulch, Alexandria Petrusich, Sandeep Soni, Mark C. Walters
Publikováno v:
Blood. 124:549-549
Background: Hematopoietic stem cell (HSC) gene therapy has the potential to induce globin production and mitigate the need for blood transfusions in β-thalassemia major. Promising early results for 2 subjects with β0/βE -thalassemia major in the o