Zobrazeno 1 - 4
of 4
pro vyhledávání: '"Johan Harris"'
Autor:
Kevin M. Flanigan, Tatyana A. Vetter, Tabatha R. Simmons, Megan Iammarino, Emma C. Frair, Federica Rinaldi, Louis G. Chicoine, Johan Harris, John P. Cheatham, Sharon L. Cheatham, Brian Boe, Megan A. Waldrop, Deborah A. Zygmunt, Davin Packer, Paul T. Martin
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 27, Iss , Pp 47-60 (2022)
In a phase 1/2, open-label dose escalation trial, we delivered rAAVrh74.MCK.GALGT2 (also B4GALNT2) bilaterally to the legs of two boys with Duchenne muscular dystrophy using intravascular limb infusion. Subject 1 (age 8.9 years at dosing) received 2.
Externí odkaz:
https://doaj.org/article/5d4cb4d3fc0f4849bd3ccf973f1e61e1
Autor:
Kevin M, Flanigan, Tatyana A, Vetter, Tabatha R, Simmons, Megan, Iammarino, Emma C, Frair, Federica, Rinaldi, Louis G, Chicoine, Johan, Harris, John P, Cheatham, Sharon L, Cheatham, Brian, Boe, Megan A, Waldrop, Deborah A, Zygmunt, Davin, Packer, Paul T, Martin
Publikováno v:
Molecular therapy. Methodsclinical development. 27
In a phase 1/2, open-label dose escalation trial, we delivered rAAVrh74.MCK.
Autor:
Margaret Beatka, Johan Harris, Brenna R. Powers, Michael W. Lawlor, Tabatha R. Simmons, Tatyana Meyers Vetter, Maryann Kaler, Emma C Frair, Megan A. Waldrop, M. Iammarino, Nico Wein, Hui Meng, Kevin M. Flanigan
Publikováno v:
Neuromuscular Disorders. 30:S166-S167
Publikováno v:
The FASEB Journal. 31