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pro vyhledávání: '"Joan LaRovere"'
Autor:
Angela Lek, Brenda Wong, Allison Keeler, Meghan Blackwood, Kaiyue Ma, Shushu Huang, Katelyn Sylvia, Ana Rita Batista, Rebecca Artinian, Danielle Kokoski, Shestruma Parajuli, Juan Putra, Chrystalle Katte Carreon, Hart Lidov, Keryn Woodman, Sander Pajusalu, Janelle Spinazzola, Thomas Gallagher, Joan LaRovere, Diane Baulderson, Lauren Black, Keith Sutton, Richard Horgan, Monkol Lek, Terence Flotte
An N-of-1 trial was developed to deliver a dCas9-VP64 transgene designed to upregulate the cortical dystrophin as a custom therapy for a Duchenne muscular dystrophy (DMD) patient. After showing signs of mild cardiac dysfunction and pericardial effusi
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::28c0f416fcddad83a5bbc110f034ef08
https://doi.org/10.1101/2023.05.16.23289881
https://doi.org/10.1101/2023.05.16.23289881
