Zobrazeno 1 - 3
of 3
pro vyhledávání: '"Jacqueline Bogedein"'
Autor:
Surabhi Kandaswamy, Lena Zobel, Bina John, Sathiyavedu Thyagarajan Santhiya, Jacqueline Bogedein, Gerhard K. H. Przemeck, Valérie Gailus-Durner, Helmut Fuchs, Martin Biel, Martin Hrabĕ de Angelis, Jochen Graw, Stylianos Michalakis, Oana Veronica Amarie
Publikováno v:
Cell Death Discovery, Vol 8, Iss 1, Pp 1-12 (2022)
Abstract Retinitis pigmentosa is a group of progressive inherited retinal dystrophies that may present clinically as part of a syndromic entity or as an isolated (nonsyndromic) manifestation. In an Indian family suffering from retinitis pigmentosa, w
Externí odkaz:
https://doaj.org/article/64371217682f4adeb05ba3804086516f
Autor:
Miranda Gehrke, Maria Diedrichs-Möhring, Jacqueline Bogedein, Hildegard Büning, Stylianos Michalakis, Gerhild Wildner
Publikováno v:
Cells, Vol 11, Iss 12, p 1881 (2022)
Objectives: AAV vectors are widely used in gene therapy, but the prevalence of neutralizing antibodies raised against AAV serotypes in the course of a natural infection, as well as innate and adaptive immune responses induced upon vector administrati
Externí odkaz:
https://doaj.org/article/929fface64ab4046a8d80532bc1be0b8
Autor:
Marina Pavlou, Christian Schön, Laurence M Occelli, Axel Rossi, Nadja Meumann, Ryan F Boyd, Joshua T Bartoe, Jakob Siedlecki, Maximilian J Gerhardt, Sabrina Babutzka, Jacqueline Bogedein, Johanna E Wagner, Siegfried G Priglinger, Martin Biel, Simon M Petersen‐Jones, Hildegard Büning, Stylianos Michalakis
Publikováno v:
EMBO Molecular Medicine, Vol 13, Iss 4, Pp n/a-n/a (2021)
Abstract Gene therapy using recombinant adeno‐associated virus (rAAV) vectors to treat blinding retinal dystrophies has become clinical reality. Therapeutically impactful targeting of photoreceptors still relies on subretinal vector delivery, which
Externí odkaz:
https://doaj.org/article/8b6c55ffca62471b9aed7b84bf31bc23