Zobrazeno 1 - 4
of 4
pro vyhledávání: '"Jacek Lukawy"'
Autor:
Laurent Servais, Eric Camino, Aude Clement, Craig M. McDonald, Jacek Lukawy, Linda P. Lowes, Damien Eggenspieler, Francesca Cerreta, Paul Strijbos
Publikováno v:
Digital Biomarkers, Vol 5, Iss 2, Pp 183-190 (2021)
Background: Functional outcome measures used to assess efficacy in clinical trials of investigational treatments for rare neuromuscular diseases like Duchenne muscular dystrophy (DMD) are performance-based tasks completed by the patient during hospit
Externí odkaz:
https://doaj.org/article/6d035a7c14754f65a79ab743a9237e5f
Publikováno v:
Journal of Neuromuscular Diseases. 9:335-346
In 2019, stride velocity 95th centile (SV95C) became the first wearable-derived digital clinical outcome assessment (COA) qualified by the European Medicines Agency (EMA) for use as a secondary endpoint in trials for Duchenne muscular dystrophy. SV95
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::71cc937a58ae1e58e6425be5dd0da700
https://doi.org/10.3233/jnd-210743
https://doi.org/10.3233/jnd-210743
Autor:
Eric Camino, Jacek Lukawy, Laurent Servais, Aude Clement, Paul Strijbos, Craig M. McDonald, Damien Eggenspieler, Francesca Cerreta, Linda Lowes
Publikováno v:
Digital Biomarkers, Vol 5, Iss 2, Pp 183-190 (2021)
Digit Biomark
Digit Biomark
Background: Functional outcome measures used to assess efficacy in clinical trials of investigational treatments for rare neuromuscular diseases like Duchenne muscular dystrophy (DMD) are performance-based tasks completed by the patient during hospit
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::65f79f64c1e51308ac4a595073d623ff
https://www.karger.com/Article/FullText/517411
https://www.karger.com/Article/FullText/517411
Autor:
Srdan Verstovsek, Jacek Lukawy, Jingjin Li, Ulrich Pirron, Bijoyesh Mookerjee, Jean-Jacques Kiladjian, Victor Sandor, Alessandro M. Vannucchi, Shui He, William M. Garrett, Kamel Malek
Publikováno v:
Journal of Clinical Oncology. 30:TPS6643-TPS6643
TPS6643^ Background: PV is a myeloproliferative neoplasm characterized by clonal stem cell proliferation, significant morbidity, shortened life span and possible evolution to myelofibrosis and acute myeloid leukemia. Splenomegaly, debilitating consti
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::5fac60c3f8cdebb6cd0a48e54569adb5
https://doi.org/10.1200/jco.2012.30.15_suppl.tps6643
https://doi.org/10.1200/jco.2012.30.15_suppl.tps6643