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pro vyhledávání: '"JA Gimeno-Blanes"'
Autor:
M Goicoechea-Diezhandino, JA García-Robles, JA Gimeno-Blanes, S Manrique-Rodríguez, María Sanjurjo-Sáez, C Pellicer-Franco, A de la Rubia-Nieto, Pernía-López
Publikováno v:
Expert Opinion on Orphan Drugs. 4:1199-1206
Objective: To describe an individualized therapeutic strategy in patients with Fabry disease receiving enzyme replacement therapy (ERT) with agalsidase beta, in order to find the minimum effective dose based on clinical outcomes and estimate its impa