Design and analysis of effects of triplet repeat oligonucleotides in cell models for myotonic dystrophy.

Autor: González-Barriga A; 1] Department of Cell Biology, Nijmegen Centre for Molecular Life Sciences, Radboud University Nijmegen Medical Centre, Nijmegen, The Netherlands [2] Prosensa Therapeutics B.V., Leiden, The Netherlands., Mulders SA, van de Giessen J, Hooijer JD, Bijl S, van Kessel ID, van Beers J, van Deutekom JC, Fransen JA, Wieringa B, Wansink DG

Publikováno v: Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2013 Mar 19; Vol. 2, pp. e81. Date of Electronic Publication: 2013 Mar 19.