Paroxysmal Cold Hemoglobinuria: Mild to Catastrophic-Spectrum of a Rare Hemolytic Anemia of Childhood.

Autor: Agarwala S; Department of Pediatric Hematology Oncology and BMT, Sir Ganga Ram Hospital., Kalra M; Department of Pediatric Hematology Oncology and BMT, Sir Ganga Ram Hospital., Sachdeva A; Department of Pediatric Hematology Oncology and BMT, Sir Ganga Ram Hospital., Anand K; Department of Pediatric Nephrology, Sir Ganga Ram Hospital., Setia R; Department of Transfusion Medicine, BLK-Max Super Specialty Hospital, New Delhi, India.

Publikováno v: Journal of pediatric hematology/oncology [J Pediatr Hematol Oncol] 2024 Nov 01; Vol. 46 (8), pp. 415-418. Date of Electronic Publication: 2024 Sep 25.

Detection of PNH Clones can Aid in the Distinction of Aplastic Anemia vs Inherited BM Failure Syndromes: A Single Center Experience and Review of the Literature.

Autor: Nasnas P; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Ling J; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Gerstein Y; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Wang SA; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Loghavi S; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Hammond D; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Montalban-Bravo G; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Senapati J; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Pemmaraju N; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Corredor J; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Pierce S; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Roth M; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Ravandi F; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Cuglievan B; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., Kadia T; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX., DiNardo CD; Department of Leukemia, The University of Texas, MD Anderson Cancer Center, Houston, TX. Electronic address: CDiNardo@mdanderson.org.

Publikováno v: Clinical lymphoma, myeloma & leukemia [Clin Lymphoma Myeloma Leuk] 2024 Oct; Vol. 24 (10), pp. 732-735. Date of Electronic Publication: 2024 Jun 12.

A growing panoply of options for patients with paroxysmal nocturnal hemoglobinuria.

Autor: Young DJ; National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, Maryland, USA.

Publikováno v: American journal of hematology [Am J Hematol] 2024 Sep; Vol. 99 (9), pp. 1667-1669. Date of Electronic Publication: 2024 Jul 18.

Comparative clinical efficacy and safety of biosimilar ABP 959 and eculizumab reference product in patients with paroxysmal nocturnal hemoglobinuria.

Autor: Kulasekararaj A; King's College Hospital NHS Foundation Trust, National Institute of Health Research/Wellcome King's Clinical Research Facility and King's College London, London, UK., Lanza F; Hematology Unit, Hospital of Ravenna, University of Bologna, Bologna, Italy., Arvanitakis A; Department of Translational Medicine, Lund University, Malmö, Sweden.; Department of Haematology, Oncology and Radiation Physics, Skane University Hospital, Malmo, Sweden., Langemeijer S; Department of Hematology, Radboud Universitair Medisch Centrum, Nijmegen, The Netherlands., Chonat S; Department of Pediatrics, Emory University and Children's Healthcare of Atlanta, Atlanta, Georgia, USA., Tombak A; Internal Medicine - Hematology Department, Mersin University, Mersin, Turkey., Hanes V; Amgen Inc, Thousand Oaks, California, USA., Cao J; Amgen Inc, Thousand Oaks, California, USA., Miller MJ; Amgen Inc, Thousand Oaks, California, USA., Colbert A; Amgen Inc, Thousand Oaks, California, USA., Shander B; Amgen Inc, Thousand Oaks, California, USA., Mytych DT; Amgen Inc, Thousand Oaks, California, USA., Chow V; Amgen Inc, Thousand Oaks, California, USA., Henary H; Amgen Inc, Thousand Oaks, California, USA.

Publikováno v: American journal of hematology [Am J Hematol] 2024 Nov; Vol. 99 (11), pp. 2108-2117. Date of Electronic Publication: 2024 Aug 22.

A machine learning algorithm for the detection of paroxysmal nocturnal haemoglobinuria (PNH) in UK primary care electronic health records.

Autor: Worker A; Mendelian, The Trampery, Old Street, London, UK. amanda@mendelian.co., Mahon H; Mendelian, The Trampery, Old Street, London, UK., Sams J; Mendelian, The Trampery, Old Street, London, UK., Boardman-Pretty F; Mendelian, The Trampery, Old Street, London, UK., Marchini E; Mendelian, The Trampery, Old Street, London, UK., Dubis R; Mendelian, The Trampery, Old Street, London, UK., Warren A; Mendelian, The Trampery, Old Street, London, UK., Stockdale J; Mendelian, The Trampery, Old Street, London, UK., Kumar J; Mendelian, The Trampery, Old Street, London, UK., Varones E; Mendelian, The Trampery, Old Street, London, UK., Ollerenshaw D; Mendelian, The Trampery, Old Street, London, UK., Grant C; Mendelian, The Trampery, Old Street, London, UK., Fish P; Mendelian, The Trampery, Old Street, London, UK., Kelly RJ; St. James's University Hospital, Leeds, UK.

Publikováno v: Orphanet journal of rare diseases [Orphanet J Rare Dis] 2024 Oct 13; Vol. 19 (1), pp. 378. Date of Electronic Publication: 2024 Oct 13.