Zobrazeno 1 - 3
of 3
pro vyhledávání: '"Grace Cooper-Olson"'
Autor:
Rachael A. Potter, Ellyn L. Peterson, Danielle Griffin, Grace Cooper Olson, Sarah Lewis, Kyle Cochran, Jerry R. Mendell, Louise R. Rodino-Klapac
Publikováno v:
Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101195- (2024)
Patients with pre-existing immunity to adeno-associated virus (AAV) are currently unable to receive systemic gene transfer therapies. In this nonhuman primate study, we investigated the impact of immunosuppression strategies on gene transfer therapy
Externí odkaz:
https://doaj.org/article/cf55b910bf664423b112cf5813d36f07
Autor:
Rachael Potter, Chris Wier, Grace Cooper-Olson, Esther Wheeler, Emily Anderbery, Amber Kempton, Leah Clements, Kaitlin Adegboye, Alex Haile, Ellyn Peterson, Louise Rodino-Klapac
Publikováno v:
Sunday, April 23.
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::0eba802d857b2ba3c2b4c4b5aee48e2d
https://doi.org/10.1212/wnl.0000000000203019
https://doi.org/10.1212/wnl.0000000000203019
Publikováno v:
Journal of Neuromuscular Diseases
Recombinant micro-dystrophin genes are designed to treat Duchenne muscular dystrophy (DMD) by retaining dystrophin domains believed to play key functional roles while fitting the packaging capacity of adeno-associated virus vectors. Domains R1-3 are
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5f20e27eeba9964488eb7dfb2072d06a
http://europepmc.org/articles/PMC8385511
http://europepmc.org/articles/PMC8385511